Lysosomal Storage Disorders
📧 Sign up to get email alerts when something new happens for Lysosomal Storage Disorders.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS research · 2026-04-24Clinical Trial Update: Genetic Studies of Lysosomal Storage Disorders
A genetic study of lysosomal storage disorders, including Gaucher disease and potentially Parkinson disease, is currently enrolling by invit…
-
CLINICAL_TRIALS research · 2017-04-04Clinical Trial Update: Investigating Lysosomal Storage Diseases in Minority Groups
A clinical trial update from O & O Alpan LLC examining lysosomal storage disorders in minority populations, including Gaucher disease, Fabry…
-
CLINICAL_TRIALS trial_result · 2014-07-08Clinical Trial Update: ALD-101 Adjuvant Therapy of Unrelated Umbilical Cord Blood Transfusion (UCBT) in Patients With Inherited Metabolic Diseases [Phase 3]
Phase 3 trial of ALD-101 as adjuvant therapy with unrelated umbilical cord blood transfusion in inherited metabolic diseases was terminated.