Lysosomal Acid Lipase Deficiency
📧 Sign up to get email alerts when something new happens for Lysosomal Acid Lipase Deficiency.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2019-11-18Clinical Trial Update: Clinical Study In Infants With Rapidly Progressive Lysosomal Acid Lipase Deficiency [Phase 2]
Phase 2 clinical trial in infants with rapidly progressive lysosomal acid lipase deficiency has been terminated; results posted in 2019.
-
CLINICAL_TRIALS trial_result · 2019-01-15Clinical Trial Update: Safety and Efficacy Study of Sebelipase Alfa in Participants With Lysosomal Acid Lipase Deficiency [Phase 2]
Phase 2 trial assessing safety and efficacy of sebelipase alfa in lysosomal acid lipase deficiency has completed with results posted.
-
CLINICAL_TRIALS trial_result · 2018-12-11Clinical Trial Update: Safety, Tolerability and Pharmacokinetics of SBC-102 (Sebelipase Alfa) in Adult Participants With Lysosomal Acid Lipase Deficiency [Phase 1, Phase 2]
Phase 1/2 trial update evaluating safety, tolerability, and pharmacokinetics of SBC-102 (Sebelipase alfa) in adults with lysosomal acid lipa…
-
CLINICAL_TRIALS trial_result · 2017-06-16Clinical Trial Update: Screening for Lysosomal Acid Lipase Deficiency
The screening trial for lysosomal acid lipase deficiency (NCT02926872) sponsored by Alexion Pharmaceuticals has been terminated.
-
CLINICAL_TRIALS trial_result · 2016-05-24Clinical Trial Update: A Study to Identify and Characterize LAL-D Patients in High-risk Populations
A terminated clinical trial update from Alexion investigating identification and characterization of patients with lysosomal acid lipase def…
- Want full summaries, importance scores, and drug timelines? Upgrade to Plus or Pro.
-
CLINICAL_TRIALS trial_result · 2016-05-09Clinical Trial Update: Extension Study to Evaluate the Long-Term Safety, Tolerability, and Efficacy of SBC-102 (Sebelipase Alfa) in Adult Subjects With Lysosomal Acid Lipase Deficiency [Phase 2]
Phase 2 extension study evaluating long-term safety, tolerability, and efficacy of Sebelipase alfa (SBC-102) in adults with lysosomal acid l…
-
CLINICAL_TRIALS trial_result · 2016-04-18Clinical Trial Update: Safety, Tolerability, Efficacy, Pharmacokinetics, and Pharmacodynamics of Sebelipase Alfa in Children With Growth Failure Due to Lysosomal Acid Lipase Deficiency [Phase 2, Phase 3]
This clinical trial update reports Phase 2/3 results for Sebelipase alfa in children with growth failure due to lysosomal acid lipase defici…
-
CLINICAL_TRIALS trial_result · 2016-04-18Clinical Trial Update: Acid Lipase Replacement Investigating Safety and Efficacy (ARISE) in Participants With Lysosomal Acid Lipase Deficiency [Phase 3]
Phase 3 trial assessing safety and efficacy of acid lipase replacement in lysosomal acid lipase deficiency has completed with results posted…