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CLINICAL_TRIALS trial_result · 2017-06-16

Clinical Trial Update: Screening for Lysosomal Acid Lipase Deficiency

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Summary

The screening trial for lysosomal acid lipase deficiency (NCT02926872) sponsored by Alexion Pharmaceuticals has been terminated.

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Diseases / indications

Drugs mentioned

  • KANUMA (Sebelipase alfa)

Snippet

Sponsor: Alexion Pharmaceuticals, Inc. | Conditions: Lysosomal Acid Lipase Deficiency | Status: TERMINATED