Limb-girdle Muscular Dystrophy Type 2d
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CLINICAL_TRIALS research · 2025-11-18Clinical Trial Update: Long-Term Development of Muscular Dystrophy Outcome Assessments
Clinical trial update indicating ongoing recruitment for a long-term study assessing outcome measures in limb-girdle muscular dystrophy acro…
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CLINICAL_TRIALS trial_result · 2025-09-04Clinical Trial Update: Study to Evaluate the Safety, Tolerability, and Efficacy of SRP-9004 Administered by Systemic Infusion in Limb Girdle Muscular Dystrophy Type 2D/R3 Participants in the United States [Phase 1]
A Phase 1 trial evaluating SRP-9004 for limb girdle muscular dystrophy type 2D/R3 has been terminated; the update concerns safety, tolerabil…
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CLINICAL_TRIALS trial_result · 2022-04-01Clinical Trial Update: A Gene Transfer Therapy Study to Evaluate the Safety of SRP-9004 (Patidistrogene Bexoparvovec) in Participants With Limb-Girdle Muscular Dystrophy, Type 2D (LGMD2D) [Phase 1, Phase 2]
Clinical trial update on SRP-9004 (patidistrogene bexoparvovec) evaluating safety in LGMD2D; study phases 1/2 have completed with results po…
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CLINICAL_TRIALS trial_result · 2013-02-05Clinical Trial Update: Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D) [Phase 1]
Phase 1 trial evaluating a gene transfer therapy for limb-girdle muscular dystrophy type 2D has completed.