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CLINICAL_TRIALS trial_result · 2025-09-04

Clinical Trial Update: Study to Evaluate the Safety, Tolerability, and Efficacy of SRP-9004 Administered by Systemic Infusion in Limb Girdle Muscular Dystrophy Type 2D/R3 Participants in the United States [Phase 1]

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Summary

A Phase 1 trial evaluating SRP-9004 for limb girdle muscular dystrophy type 2D/R3 has been terminated; the update concerns safety, tolerability, and potential e…

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Diseases / indications

Drugs mentioned

  • SRP-9004

Snippet

Sponsor: Sarepta Therapeutics, Inc. | Conditions: Limb Girdle Muscular Dystrophy, Limb Girdle Muscular Dystrophy Type 2D/R3 | Phase 1 | Status: TERMINATED