Hypochondroplasia
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CLINICAL_TRIALS research · 2026-03-31Clinical Trial Update: A Study of Vosoritide Versus Placebo in Children With Hypochondroplasia Aged 0 to < 36 Months [Phase 2]
A Phase 2 study evaluating Vosoritide versus placebo in children with hypochondroplasia aged 0 to < 36 months is currently recruiting.
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CLINICAL_TRIALS research · 2026-02-20Clinical Trial Update: Prospective Longitudinal Monocentric Study to Measure Limb Movement in Patients With FGFR3-related Skeletal Dysplasia
Prospective, monocentric study sponsored by SYSNAV to measure limb movement in patients with FGFR3-related skeletal dysplasia. Recruitment i…
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CLINICAL_TRIALS trial_result · 2026-02-06Clinical Trial Update: Open-Label, Long-Term, Extension Study of Infigratinib in Children With Hypochondroplasia [Phase 2]
Open-label, long-term extension study of infigratinib in children with hypochondroplasia is currently enrolling by invitation.
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CLINICAL_TRIALS research · 2026-01-20Clinical Trial Update: Interventional Study of Vosoritide for the Treatment of Children With Hypochondroplasia [Phase 3]
A Phase 3 interventional trial evaluating Vosoritide for hypochondroplasia in children is active but not recruiting. This document updates t…
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CLINICAL_TRIALS research · 2025-12-15Clinical Trial Update: An Interventional Study of Infigratinib in Children With Hypochondroplasia [Phase 2, Phase 3]
Interventional Phase 2/3 study of Infigratinib in children with hypochondroplasia is currently enrolling by invitation.
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CLINICAL_TRIALS research · 2025-10-10Clinical Trial Update: Prospective Clinical Assessment Study in Children With Hypochondroplasia
Clinical trial update for a prospective study in children with hypochondroplasia; recruitment is ongoing.
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CLINICAL_TRIALS trial_result · 2025-07-18Clinical Trial Update: Long-Term Extension Study of Vosoritide to Treat Children With Hypochondroplasia [Phase 3]
An ongoing long-term extension (Phase 3) study is evaluating Vosoritide in children with hypochondroplasia to assess long-term safety and ef…
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CLINICAL_TRIALS research · 2025-04-03Clinical Trial Update: A Multicenter Multinational Observational Study of Children With Hypochondroplasia
Multicenter multinational observational study in children with hypochondroplasia sponsored by BioMarin Pharmaceutical; currently recruiting.
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CLINICAL_TRIALS trial_result · 2019-02-15Clinical Trial Update: Efficacy and Safety Evaluation of Recombinant Human Growth Hormone (r-hGH), Saizen®, on a Population of Children With Hypochondroplasia, Treated at Least 3 Years or Until Near Final Height, When Applicable, in Comparison With a Historic Cohort of Non-treated Children [Phase 2]
A Phase 2 trial evaluated the efficacy and safety of recombinant human growth hormone (Saizen) in children with hypochondroplasia treated fo…
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CLINICAL_TRIALS trial_result · 2015-04-14Clinical Trial Update: C-Type Natriuretic Peptide and Achondroplasia
This update reports the completion of a clinical trial investigating C-type natriuretic peptide for achondroplasia and hypochondroplasia.