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CLINICAL_TRIALS trial_result · 2025-07-18

Clinical Trial Update: Long-Term Extension Study of Vosoritide to Treat Children With Hypochondroplasia [Phase 3]

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Summary

An ongoing long-term extension (Phase 3) study is evaluating Vosoritide in children with hypochondroplasia to assess long-term safety and efficacy.

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Diseases / indications

Drugs mentioned

  • Vosoritide (vosoritide)

Snippet

Sponsor: BioMarin Pharmaceutical | Conditions: Hypochondroplasia | Phase 3 | Status: ENROLLING_BY_INVITATION