CLINICAL_TRIALS
trial_result
· 2025-07-18
Clinical Trial Update: Long-Term Extension Study of Vosoritide to Treat Children With Hypochondroplasia [Phase 3]
Summary
An ongoing long-term extension (Phase 3) study is evaluating Vosoritide in children with hypochondroplasia to assess long-term safety and efficacy.
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Drugs mentioned
Snippet
Sponsor: BioMarin Pharmaceutical | Conditions: Hypochondroplasia | Phase 3 | Status: ENROLLING_BY_INVITATION