Hurler-scheie Syndrome
📧 Sign up to get email alerts when something new happens for Hurler-scheie Syndrome.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS research · 2026-03-12Clinical Trial Update: RGX-111 Gene Therapy in Patients With MPS I [Phase 1, Phase 2]
The RGX-111 gene therapy trial for Mucopolysaccharidosis Type I is currently suspended in Phase 1/2.