CLINICAL_TRIALS
research
· 2026-03-12
Clinical Trial Update: RGX-111 Gene Therapy in Patients With MPS I [Phase 1, Phase 2]
Summary
The RGX-111 gene therapy trial for Mucopolysaccharidosis Type I is currently suspended in Phase 1/2.
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Snippet
Sponsor: REGENXBIO Inc. | Conditions: Mucopolysaccharidosis Type I (MPS I), Hurler Syndrome | Phase 1, Phase 2 | Status: SUSPENDED