Hereditary Amyloidosis
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-01-05Clinical Trial Update: Myocardial Effects in Patients With ATTRv With Polyneuropathy Treated With Patisiran or Vutrisiran
Clinical trial update describing myocardial effects observed in patients with hereditary transthyretin-mediated amyloidosis with polyneuropa…
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CLINICAL_TRIALS research · 2025-06-04Clinical Trial Update: Subclinical Transthyretin Cardiac Amyloidosis in V122I TTR Carriers
A clinical trial is recruiting to study subclinical transthyretin cardiac amyloidosis in individuals carrying the V122I TTR mutation.