Hereditary Amyloidosis

• CLINICAL_TRIALS research · 2026-01-05
  Clinical Trial Update: Myocardial Effects in Patients With ATTRv With Polyneuropathy Treated With Patisiran or Vutrisiran

  Clinical trial update describing myocardial effects observed in patients with hereditary transthyretin-mediated amyloidosis with polyneuropa…

• CLINICAL_TRIALS research · 2025-06-04
  Clinical Trial Update: Subclinical Transthyretin Cardiac Amyloidosis in V122I TTR Carriers

  A clinical trial is recruiting to study subclinical transthyretin cardiac amyloidosis in individuals carrying the V122I TTR mutation.

• CLINICAL_TRIALS trial_result · 2018-09-06
  Clinical Trial Update: APOLLO: The Study of an Investigational Drug, Patisiran (ALN-TTR02), for the Treatment of Transthyretin (TTR)-Mediated Amyloidosis [Phase 3]

  Phase 3 study of patisiran (ALN-TTR02) for transthyretin-mediated amyloidosis has completed with results posted in 2018.