Hemophilia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2019-04-11Clinical Trial Update: Study of Recombinant Factor IX Product, IB1001, in Previously Treated Pediatric Subjects With Hemophilia B [Phase 3]
A Phase 3 study of IB1001, a recombinant factor IX product, was terminated in previously treated pediatric subjects with Hemophilia B.
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CLINICAL_TRIALS trial_result · 2019-04-10Clinical Trial Update: A Study of Emicizumab Administered Subcutaneously (SC) in Pediatric Participants With Hemophilia A and Factor VIII (FVIII) Inhibitors [Phase 3]
Phase 3 study update on subcutaneous emicizumab in pediatric Hemophilia A patients with FVIII inhibitors; trial completed with posted result…
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CLINICAL_TRIALS trial_result · 2019-02-18Clinical Trial Update: Individualizing Hemophilia Prophylaxis Using Thromboelastography [NA]
The report describes a completed study evaluating individualized prophylaxis for Hemophilia A using thromboelastography.
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CLINICAL_TRIALS trial_result · 2019-02-15Clinical Trial Update: Efficacy of Strength Training in Improving Elbow Range of Motion and Function in Adults With Hemophilia [NA]
A completed clinical trial evaluating whether structured strength training improves elbow range of motion and function in adults with hemoph…
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CLINICAL_TRIALS research · 2019-01-29Clinical Trial Update: Evaluation of a Standardized Protocol for Thrombin Generation Assay
A Lund University study evaluating a standardized thrombin generation assay protocol in Hemophilia A has completed.
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FDA approval · 2019-01-28FDA Approved: DESMOPRESSIN ACETATE — Original Application (KVK-TECH, INC.)
The FDA approved Desmopressin Acetate from KVK-Tech under an Original Application, providing a new generic option for this drug product.
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CLINICAL_TRIALS trial_result · 2019-01-11Clinical Trial Update: Study Evaluating Prophylaxis Treatment & Characterizing Efficacy, Safety, & PK Of B-Domain Deleted Recombinant FVIII [Phase 3]
Phase 3 trial update evaluating prophylaxis and efficacy, safety, and pharmacokinetics of a B-domain deleted recombinant Factor VIII for Hem…
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CLINICAL_TRIALS trial_result · 2018-12-26Clinical Trial Update: A Study to Evaluate the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of Emicizumab Given Every 4 Weeks in Participants With Hemophilia A [Phase 3]
Phase 3 clinical trial evaluating emicizumab every 4 weeks in adults and children with Hemophilia A has completed; results posted in 2018.
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CLINICAL_TRIALS trial_result · 2018-12-06Clinical Trial Update: A Trial Investigating Safety and Efficacy of Treatment With BAY94-9027 in Severe Hemophilia A [Phase 2, Phase 3]
A completed Phase 2/3 trial evaluating BAY94-9027 for safety and efficacy in severe Hemophilia A has posted results.
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FDA approval · 2018-11-27FDA Approved: AMINOCAPROIC ACID — Original Application (Vitruvias Therapeutics)
FDA approved Vitruvias Therapeutics' original application for aminocaproic acid, a generic antifibrinolytic. The approval covers its use to …
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CLINICAL_TRIALS trial_result · 2018-11-23Clinical Trial Update: Long-Term Safety and Efficacy of rFIXFc in the Prevention and Treatment of Bleeding Episodes in Previously Treated Participants With Hemophilia B [Phase 3]
Phase 3 trial update evaluating long-term safety and efficacy of rFIXFc for prevention and treatment of bleeding in previously treated parti…
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CLINICAL_TRIALS trial_result · 2018-11-23Clinical Trial Update: Long-Term Safety and Efficacy of rFVIIIFc in the Prevention and Treatment of Bleeding Episodes in Previously Treated Participants With Hemophilia A [Phase 3]
Phase 3 trial assessing long-term safety and efficacy of rFVIIIFc for prevention and treatment of bleeding in previously treated participant…
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CLINICAL_TRIALS trial_result · 2018-11-14Clinical Trial Update: A Clinical Trial to Evaluate Prophylactic Emicizumab Versus no Prophylaxis in Hemophilia A Participants Without Inhibitors [Phase 3]
Phase 3 trial evaluating prophylactic emicizumab versus no prophylaxis in Hemophilia A patients without inhibitors has completed with result…
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CLINICAL_TRIALS trial_result · 2018-11-14Clinical Trial Update: Safety and Dose Finding Study of DTX101 (AAVrh10FIX) in Adults With Moderate/Severe to Severe Hemophilia B [Phase 1, Phase 2]
A safety and dose-finding study of DTX101 (AAVrh10FIX) in adults with Hemophilia B was terminated; results were posted in 2018.
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CLINICAL_TRIALS trial_result · 2018-11-07Clinical Trial Update: Clinical Trial of Factor XIII (FXIII) Concentrate [NA]
Completed clinical trial of Factor XIII concentrate for hemophilia and Factor XIII deficiency; results posted in 2018.
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FDA approval · 2018-10-04FDA Approved: HEMLIBRA — Supplemental Application (Genentech, Inc.)
FDA approved a supplemental application for Hemlibra (emicizumab) submitted by Genentech, Inc.
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CLINICAL_TRIALS withdrawal · 2018-09-25Clinical Trial Update: Study Comparing Blood Levels of ReFacto and Advante in Hemophilia A [Phase 4]
A Phase 4 trial comparing blood levels of ReFacto and Advante in Hemophilia A was withdrawn.
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CLINICAL_TRIALS trial_result · 2018-09-25Clinical Trial Update: Evaluation Of Acceptability And Satisfaction Of Hemophilia Patients Treated With FusENGO
A completed clinical trial evaluating acceptability and satisfaction among hemophilia patients treated with FusENGO (Pfizer sponsor).
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CLINICAL_TRIALS trial_result · 2018-09-24Clinical Trial Update: Registry For Patients Treated With BeneFix In Usual Care Setting In Germany
A registry trial update for BeneFix in the usual care setting in Germany for Hemophilia B, with completed status and posted results.
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CLINICAL_TRIALS trial_result · 2018-09-20Clinical Trial Update: BAX 826 Dose-Escalation Safety Study [Phase 1]
Phase 1 dose-escalation safety study of BAX 826 for Hemophilia A has completed; results posted.
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CLINICAL_TRIALS trial_result · 2018-09-10Clinical Trial Update: BAX 326 (rFIX) Continuation Study [Phase 3]
Phase 3 continuation study of BAX 326 (recombinant factor IX) for Hemophilia B completed; results posted in 2018.
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CLINICAL_TRIALS trial_result · 2018-09-10Clinical Trial Update: Study of Recombinant Factor IX Product, IB1001, in Subjects With Hemophilia B [Phase 2, Phase 3]
Phase 2/Phase 3 trial update for recombinant Factor IX product IB1001 in Hemophilia B completed with results posted.
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CLINICAL_TRIALS trial_result · 2018-08-14Clinical Trial Update: Pharmacokinetic (PK)Research on Chinese Children of Hemophilia [Phase 4]
Phase 4 pharmacokinetic study evaluating hemophilia-related PK in Chinese pediatric patients.
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CLINICAL_TRIALS trial_result · 2018-07-26Clinical Trial Update: Low-dose ITI Strategy for Children in Hemophilia A With High-titer Inhibitor and Poor ITI Risk in China [Phase 4]
A Phase 4 clinical trial is evaluating a low-dose immune tolerance induction strategy for children with Hemophilia A and inhibitors who are …
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CLINICAL_TRIALS trial_result · 2018-07-17Clinical Trial Update: Study Evaluating Pharmacovigilance Of Refacto AF
A completed pharmacovigilance study evaluating Refacto AF in Hemophilia A; results were posted on 2018-07-17.