Hemophilia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2020-10-08Clinical Trial Update: Once-A-Day Prophylaxis for Youth and Young Adults With Severe Hemophilia A [Phase 2]
Phase 2 clinical trial update on once-daily prophylaxis for youth and young adults with severe Hemophilia A.
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CLINICAL_TRIALS trial_result · 2020-09-25Clinical Trial Update: Weight-based Dosing in Hemophilia A [Phase 2]
Phase 2 trial investigating weight-based dosing in Hemophilia A has terminated with posted results.
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CLINICAL_TRIALS trial_result · 2020-09-17Clinical Trial Update: Platelet-Rich Plasma Intra-Articular Injection in Treating Hemophilic Arthropathy [NA]
A completed clinical trial evaluating platelet-rich plasma intra-articular injections for treating hemophilic arthropathy; results posted in…
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CLINICAL_TRIALS trial_result · 2020-08-21Clinical Trial Update: Safety and Efficacy of BAY94-9027 in Previously Treated Male Children With Haemophilia A [Phase 3]
Phase 3 trial updating safety and efficacy of BAY94-9027 in previously treated male children with Hemophilia A has completed.
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CLINICAL_TRIALS trial_result · 2020-08-13Clinical Trial Update: An Open Label Study to Determine the Safety and Efficacy of Replacement Factor VIII Protein (Known as rFVIIIFc) in Previously Untreated Males With Severe Hemophilia A [Phase 3]
Phase 3 open-label trial assessing safety and efficacy of replacement factor VIII (rFVIIIFc) in previously untreated males with severe Hemop…
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CLINICAL_TRIALS trial_result · 2020-07-31Clinical Trial Update: Study to Determine the Safety and Efficacy of rFIXFc in Previously Untreated Males With Severe Hemophilia B [Phase 3]
A Phase 3 trial evaluating safety and efficacy of rFIXFc in previously untreated males with severe Hemophilia B has completed and posted res…
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CLINICAL_TRIALS trial_result · 2020-06-16Clinical Trial Update: Study of Ataluren (PTC124) in Hemophilia A and B [Phase 2]
Phase 2 trial of ataluren (PTC124) in Hemophilia A and B was terminated; results posted in 2020.
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CLINICAL_TRIALS trial_result · 2020-05-29Clinical Trial Update: INdividualized ITI Based on Fviii(ATE) Protection by VWF [Phase 4]
Phase 4 trial update for individualized ITI based on FVIII protection by von Willebrand factor in Hemophilia A patients with inhibitors; tri…
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CLINICAL_TRIALS trial_result · 2020-05-19Clinical Trial Update: A Gene Therapy Study for Hemophilia B [Phase 2]
Phase 2 gene therapy trial for Hemophilia B completed; results posted in 2020.
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CLINICAL_TRIALS trial_result · 2020-04-28Clinical Trial Update: Safety and Efficacy of Long-term Treatment With SCT800 in Previously Treated Hemophilia A Patients. [Phase 4]
Phase 4 trial update assessing long-term safety and efficacy of SCT800 in previously treated Hemophilia A patients.
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CLINICAL_TRIALS trial_result · 2020-03-24Clinical Trial Update: Prospective Biomarkers of Bone Metabolism in Hemophilia A [Phase 3]
A Phase 3 trial evaluating prospective biomarkers of bone metabolism in individuals with Hemophilia A has completed with results posted.
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CLINICAL_TRIALS trial_result · 2020-02-25Clinical Trial Update: Exercise Versus DDAVP in Patients With Mild Hemophilia A [Phase 4]
A Phase 4 clinical trial comparing exercise versus DDAVP in patients with mild Hemophilia A has completed.
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CLINICAL_TRIALS trial_result · 2020-02-06Clinical Trial Update: Evaluation of SCT800 in Prophylaxis Therapy on Previous Treated Patients With Severe Hemophilia A [Phase 3]
Phase 3 clinical trial evaluating SCT800 for prophylaxis in previously treated patients with severe Hemophilia A has completed.
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CLINICAL_TRIALS trial_result · 2019-12-24Clinical Trial Update: Pharmacokinetics, Efficacy, Safety, and Immunogenicity of Wilate in Previously Treated Paediatric Patients With Severe Haemophilia A [Phase 3]
Phase 3 trial update evaluating pharmacokinetics, efficacy, safety, and immunogenicity of Wilate in previously treated paediatric patients w…
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CLINICAL_TRIALS trial_result · 2019-12-17Clinical Trial Update: Study to Investigate Immunogenicity, Efficacy and Safety of Treatment With Human-cl rhFVIII [Phase 3]
Phase 3 trial update evaluating immunogenicity, efficacy, and safety of human-cl rhFVIII in severe Hemophilia A; results posted after comple…
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CLINICAL_TRIALS trial_result · 2019-12-05Clinical Trial Update: Canadian Hemophilia Prophylaxis Study [Phase 4]
Phase 4 clinical trial update for prophylaxis in severe Hemophilia A; study completed with results posted in 2019.
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CLINICAL_TRIALS trial_result · 2019-12-04Clinical Trial Update: PF-06741086 Multiple Dose Study in Severe Hemophilia [Phase 2]
Phase 2 multiple-dose study of PF-06741086 in severe hemophilia completed with results posted.
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CLINICAL_TRIALS trial_result · 2019-12-03Clinical Trial Update: Clinical Study to Investigate the PK, Efficacy, and Safety of Wilate in Patients With Severe Hemophilia A [Phase 3]
Phase 3 clinical study completed evaluating PK, efficacy, and safety of Wilate in patients with severe hemophilia A, with results posted.
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CLINICAL_TRIALS trial_result · 2019-12-03Clinical Trial Update: Assess the Efficacy and Safety of Personalized Prophylaxis Human-cl rhFVIII in Patients With Severe Haemophilia A [Phase 3]
Phase 3 trial evaluating personalized prophylaxis with human-cl rhFVIII in severe hemophilia A has completed and results were posted.
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CLINICAL_TRIALS trial_result · 2019-12-02Clinical Trial Update: A Safety, Tolerability, and Pharmacokinetics Study of a Single Intravenous Injection of Recombinant Coagulation Factor VIII Fc - Von Willebrand Factor - XTEN Fusion Protein (rFVIIIFc-VWF-XTEN) (BIVV001) in Previously Treated Adults With Severe Hemophilia A (EXTEN-A) [Phase 1, Phase 2]
Phase 1/2 study evaluating safety, tolerability, and pharmacokinetics of a single IV dose of rFVIIIFc-VWF-XTEN (BIVV001) in previously treat…
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CLINICAL_TRIALS trial_result · 2019-10-31Clinical Trial Update: Patient Reported Outcomes Burdens and Experiences - Phase 2
Phase 2 clinical trial update focusing on patient-reported outcomes, burdens, and experiences in hemophilia.
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CLINICAL_TRIALS trial_result · 2019-10-21Clinical Trial Update: Human Cell Line-derived Recombinant Factor VIII (Human-cl-rhFVIII) in Previously Untreated Patients [Phase 3]
Phase 3 trial update on Human cell line-derived recombinant Factor VIII in previously untreated patients with severe Hemophilia A; results p…
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CLINICAL_TRIALS trial_result · 2019-09-30Clinical Trial Update: A Study to Investigate the Pharmacokinetics, Safety, and Tolerability of Emicizumab in Healthy Chinese Volunteers [Phase 1]
Phase 1 pharmacokinetics and safety study of emicizumab in healthy Chinese volunteers completed.
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CLINICAL_TRIALS trial_result · 2019-09-06Clinical Trial Update: LR769 in Congenital Hemophilia Patients With Inhibitors Undergoing Elective Surgery or Invasive Procedures [Phase 3]
A Phase 3 clinical trial update for LR769 in congenital hemophilia patients with inhibitors undergoing elective surgery or invasive procedur…
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CLINICAL_TRIALS trial_result · 2019-08-26Clinical Trial Update: BAX 855 PK-guided Dosing [Phase 3]
A Phase 3 trial update on PK-guided dosing for BAX 855 in Hemophilia A has completed with results posted in 2019.