Hemophilia
📧 Sign up to get email alerts when something new happens for Hemophilia.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2023-10-05Clinical Trial Update: Preventing Inhibitor Recurrence Indefinitely [Phase 4]
A Phase 4 clinical trial update on strategies to prevent inhibitor recurrence indefinitely in patients with Hemophilia A undergoing immune t…
-
CLINICAL_TRIALS trial_result · 2023-08-29Clinical Trial Update: Phase III Expansion Trial for Determining the Safety and Efficacy of Recombinant Human Coagulation Factor VIII-Fc Fusion Protein for Injection in Adolescent and Adult Patients With Hemophilia A [Phase 3]
Phase III expansion trial evaluating the safety and efficacy of Recombinant Human Coagulation Factor VIII-Fc Fusion Protein for injection in…
-
CLINICAL_TRIALS trial_result · 2023-07-07Clinical Trial Update: Study to Evaluate Safety and Tolerability of a Single Dose of PF-06741086 in Chinese Adult Participants With Severe Hemophilia [Phase 1]
Phase 1 trial completed evaluating safety and tolerability of a single dose of PF-06741086 in Chinese adults with severe hemophilia.
-
CLINICAL_TRIALS trial_result · 2023-06-28Clinical Trial Update: Study to Gain More Information on How Safe and Effective Jivi Works in Patients With Severe Hemophilia A (Post-marketing Investigation) [Phase 4]
Phase 4 post-marketing study updating safety and efficacy information for Jivi in patients with severe Hemophilia A.
-
CLINICAL_TRIALS trial_result · 2023-05-24Clinical Trial Update: A Phase 3 Open-label Interventional Study of Intravenous Recombinant Coagulation Factor VIII Fc-von Willebrand Factor-XTEN Fusion Protein, Efanesoctocog Alfa (BIVV001), in Patients With Severe Hemophilia A [Phase 3]
Phase 3 open-label interventional study evaluating intravenous efanesoctocog alfa (BIVV001) in severe hemophilia A has completed with result…
- Want full summaries, importance scores, and drug timelines? Upgrade to Plus or Pro.
-
CLINICAL_TRIALS trial_result · 2023-05-15Clinical Trial Update: A Study of Repeat Dosing of PEG Recombinant Human Coagulation Factor VIII-Fc Fusion Protein for Injection [Phase 2]
Phase 2 study update on repeat dosing of PEG Recombinant Human Coagulation Factor VIII-Fc Fusion Protein for injection in severe hemophilia …
-
CLINICAL_TRIALS trial_result · 2023-04-11Clinical Trial Update: The Hemophilia Inhibitor Prevention Trial [Phase 3]
Phase 3 trial update for Hemophilia A without inhibitors; study status terminated with results posted in 2023.
-
CLINICAL_TRIALS trial_result · 2023-02-21Clinical Trial Update: The Hemophilia Inhibitor Eradication Trial [Phase 3]
Phase 3 trial in Hemophilia A with inhibitor was terminated; results posted in 2023.
-
CLINICAL_TRIALS trial_result · 2023-02-15Clinical Trial Update: Impact of Moderate Intensity Physical Activities on PK-guided EHL FVIII Concentrates Prophylaxis Severe HA Patients [Phase 4]
Phase 4 trial assessing how moderate-intensity physical activity affects PK-guided extended half-life factor VIII concentrates for prophylax…
-
CLINICAL_TRIALS trial_result · 2023-02-06Clinical Trial Update: A Study of Fitusiran in Severe Hemophilia A and B Patients Previously Receiving Factor or Bypassing Agent Prophylaxis [Phase 3]
Phase 3 trial evaluating fitusiran in severe hemophilia A and B patients previously on factor or bypassing agent prophylaxis has completed w…
-
CLINICAL_TRIALS trial_result · 2022-12-15Clinical Trial Update: A Study to Evaluate the Safety, Efficacy, Pharmacokinetics and Pharmacodynamics of Emicizumab in Participants With Mild or Moderate Hemophilia A Without FVIII Inhibitors [Phase 3]
Phase 3 study evaluating safety, efficacy, pharmacokinetics and pharmacodynamics of emicizumab in people with Hemophilia A without FVIII inh…
-
CLINICAL_TRIALS trial_result · 2022-12-02Clinical Trial Update: A Factor IX Gene Therapy Study (FIX-GT) [Phase 1, Phase 2]
A phase 1/2 clinical trial of a Factor IX gene therapy (FIX-GT) for Hemophilia B was terminated; results were posted in 2022.
-
CLINICAL_TRIALS trial_result · 2022-10-10Clinical Trial Update: HOPE-B: Trial of AMT-061 in Severe or Moderately Severe Hemophilia B Patients [Phase 3]
The HOPE-B Phase 3 trial of AMT-061 (fidanacogene elaparvovec) for Hemophilia B has completed, with results posted in October 2022.
-
CLINICAL_TRIALS trial_result · 2022-08-30Clinical Trial Update: RIXUBIS PMS India (RIXUBIS PMS) [Phase 4]
Phase 4 trial update for RIXUBIS in Hemophilia B; study completed with results posted.
-
CLINICAL_TRIALS trial_result · 2022-08-04Clinical Trial Update: Clinical Study of Recombinant Human Activated Coagulation Factor VII for Injection in Patients With Hemophilia With Inhibitor [Phase 3]
Phase 3 clinical study evaluating recombinant human activated coagulation factor VII for injection in patients with hemophilia with inhibito…
-
CLINICAL_TRIALS trial_result · 2022-07-20Clinical Trial Update: Clinical Outcomes of Low Dose PK-guided EHL FVIII Concentrates Versus Standard Prophylaxis in Severe Haemophilia A [Phase 4]
A Phase 4 trial comparing low-dose PK-guided extended-half-life FVIII concentrates to standard prophylaxis in adults with severe Hemophilia …
-
CLINICAL_TRIALS trial_result · 2022-07-14Clinical Trial Update: A Safety and Efficacy Extension Study of a Recombinant Fusion Protein Linking Coagulation Factor IX With Albumin (rIX-FP) in Patients With Hemophilia B [Phase 3]
A Phase 3 extension study evaluated the safety and efficacy of rIX-FP in patients with Hemophilia B.
-
CLINICAL_TRIALS trial_result · 2022-07-01Clinical Trial Update: A Study to Evaluate the Safety and Efficacy of VGB-R04 in Adult Hemophilia B Patients [Phase 1, Phase 2]
A study evaluating the safety and efficacy of VGB-R04 in adults with Hemophilia B is currently in Phase 1/2 with unknown status.
-
CLINICAL_TRIALS trial_result · 2022-06-27Clinical Trial Update: Trial of AAV5-hFIX in Severe or Moderately Severe Hemophilia B [Phase 1, Phase 2]
Phase 1/2 trial of AAV5-hFIX in severe or moderately severe Hemophilia B has completed; results posted in 2022.
-
CLINICAL_TRIALS trial_result · 2022-06-16Clinical Trial Update: Dose Confirmation Trial of AAV5-hFIXco-Padua [Phase 2]
Phase 2 dose confirmation trial of AAV5-hFIXco-Padua for Hemophilia B has completed and results have been posted.
-
CLINICAL_TRIALS trial_result · 2022-06-09Clinical Trial Update: Safety Study of Alphanate in Previously Treated Patients With Severe Hemophilia A [Phase 4]
This is a Phase 4 safety study of Alphanate in previously treated patients with severe Hemophilia A. Results have been posted.
-
CLINICAL_TRIALS trial_result · 2022-05-19Clinical Trial Update: A Phase 1/2 Study of SHP648, an Adeno-Associated Viral Vector for Gene Transfer in Hemophilia B Subjects [Phase 1, Phase 2]
Phase 1/2 trial of SHP648, an AAV-based gene transfer for Hemophilia B, is terminated with results posted.
-
CLINICAL_TRIALS trial_result · 2022-03-09Clinical Trial Update: A Study to Evaluate the Safest Dose Range for FEIBA in Hemophilia A Patients With Inhibitors on Emicizumab [Phase 4]
A Phase 4 clinical trial to evaluate the safest dose range for FEIBA in hemophilia A patients with inhibitors who are on emicizumab.
-
CLINICAL_TRIALS trial_result · 2022-02-04Clinical Trial Update: A Study of Fitusiran (ALN-AT3SC) in Severe Hemophilia A and B Patients Without Inhibitors [Phase 3]
Phase 3 trial of Fitusiran in severe Hemophilia A and B patients without inhibitors completed; results posted in 2022.
-
CLINICAL_TRIALS trial_result · 2021-12-21Clinical Trial Update: A Study of Fitusiran (ALN-AT3SC) in Severe Hemophilia A and B Patients With Inhibitors [Phase 3]
Phase 3 trial update for fitusiran (ALN-AT3SC) in severe Hemophilia A and B patients with inhibitors has completed with results posted.