Hemophilia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-04-07Clinical Trial Update: A Clinical Study to Evaluate the Effects of NXT007 Compared to Emicizumab Prophylaxis in People With Hemophilia A [Phase 3]
Phase 3 clinical trial comparing NXT007 to Emicizumab prophylaxis in people with Hemophilia A; the study is currently recruiting.
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CLINICAL_TRIALS research · 2026-04-07Clinical Trial Update: Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively [Phase 3]
Phase 3 trials are evaluating the safety and effectiveness of Giroctocogene Fitelparvovec for Hemophilia A and Fidanacogene Elaparvovec for …
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CLINICAL_TRIALS research · 2026-04-06Clinical Trial Update: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of NXT007 in Persons With Severe or Moderate Hemophilia A [Phase 1, Phase 2]
This is an ongoing Phase 1/2 clinical trial evaluating NXT007 in adults with Hemophilia A, assessing safety, tolerability, pharmacokinetics,…
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CLINICAL_TRIALS research · 2026-04-06Clinical Trial Update: Pharmacokinetics, Pharmacodynamics, and Safety Profile of Understudied Drugs Administered to Children Per Standard of Care (POPS)
Duke University-sponsored trial evaluating pharmacokinetics, pharmacodynamics, and safety of understudied drugs given to children as part of…
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CLINICAL_TRIALS research · 2026-04-03Clinical Trial Update: Emicizumab for Severe Von Willebrand Disease (VWD) and VWD/Hemophilia A [Phase 1]
A Phase 1 clinical trial is evaluating Emicizumab (Hemlibra) for severe Von Willebrand disease (type 3) and for patients with concomitant Vo…
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CLINICAL_TRIALS research · 2026-03-31Clinical Trial Update: A Gene Therapy Study of SPK-8011QQ in Adults With Severe or Moderately Severe Hemophilia A [Phase 1, Phase 2]
A phase 1/2 gene therapy study (SPK-8011QQ) in adults with severe or moderately severe Hemophilia A, sponsored by Hoffmann-La Roche, is not …
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CLINICAL_TRIALS research · 2026-03-30Clinical Trial Update: A Study to Learn About How Changing Therapy From Emicizumab to Marstacimab Affects People With the Severe Hemophilia A. [Phase 1]
A Phase 1 study evaluating the effects of switching from emicizumab to marstacimab in people with severe hemophilia A.
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CLINICAL_TRIALS research · 2026-03-30Clinical Trial Update: A Study to Learn About the Study Medicine -Hympavzi in Congenital Hemophilia Patients Without Inhibitors in Japan.
A clinical trial to study Hympavzi in congenital hemophilia A or B patients without inhibitors in Japan; the study is currently active but n…
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CLINICAL_TRIALS research · 2026-03-24Clinical Trial Update: Long-term Study Evaluating Joint Health in People With Haemophilia A Receiving Real-world Prophylactic Treatment With Efanesoctocog Alfa [Phase 4]
This is a Phase 4 clinical trial update evaluating long-term joint health in people with Hemophilia A who are receiving real-world prophylax…
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CLINICAL_TRIALS research · 2026-03-23Clinical Trial Update: Monitoring of Anti-TFPI in Hemophilia
A clinical trial is monitoring an anti-TFPI therapy for hemophilia, and the study is currently recruiting.
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CLINICAL_TRIALS research · 2026-03-19Clinical Trial Update: A Trial That Evaluates Disease Characteristics in Hemophilia B Adult Male Participants Receiving Prophylaxis With Standard of Care Factor IX Protein (FIX) Replacement Therapy
Clinical trial update describing a study that evaluates disease characteristics in adult male participants with Hemophilia B receiving proph…
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CLINICAL_TRIALS research · 2026-03-17Clinical Trial Update: Evaluation of the Safety and Efficacy of Hemophilia A Gene Therapy Drugs [Phase 2, Phase 3]
Ongoing Phase 2/Phase 3 clinical trials are evaluating the safety and efficacy of a gene therapy for Hemophilia A, sponsored by Shanghai Xin…
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CLINICAL_TRIALS research · 2026-03-17Clinical Trial Update: Efficacy and Safety of CSL222 (Etranacogene Dezaparvovec) Gene Therapy in Adults With Hemophilia B With Pretreatment Adeno-associated Virus Serotype 5 (AAV5) Neutralizing Antibodies (Nabs) [Phase 3]
This Phase 3 trial evaluates the efficacy and safety of CSL222 (etranacogene dezaparvovec) gene therapy for adults with Hemophilia B who hav…
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CLINICAL_TRIALS research · 2026-03-11Clinical Trial Update: The CACHE Study: Coronary Artery Care in HaEmophilia
The CACHE Study is a recruiting clinical trial at Oxford University Hospitals NHS Trust evaluating coronary artery care in patients with Hem…
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CLINICAL_TRIALS research · 2026-03-06Clinical Trial Update: EPOCH-Economics and Patient Outcomes in China in Haemophilia
This clinical trial update discusses the EPOCH economic analysis and patient outcomes in China for hemophilia, with the study currently acti…
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CLINICAL_TRIALS research · 2026-02-27Clinical Trial Update: Efficacy and Safety Evaluation Study of SCT800 in Previously Untreated Hemophilia A Patients. [Phase 3]
A Phase 3 clinical trial evaluating the efficacy and safety of SCT800 in previously untreated patients with Hemophilia A is currently recrui…
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CLINICAL_TRIALS research · 2026-02-20Clinical Trial Update: Validity and Reliability of the Two-minute Step Test in Hemophilia
A clinical trial evaluating the validity and reliability of the Two-minute Step Test in people with hemophilia; the study is currently not y…
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CLINICAL_TRIALS research · 2026-02-20Clinical Trial Update: Effectiveness of an Educational Program for Pain Management in Patients With Hemophilic Arthropathy [NA]
This clinical trial aims to evaluate the effectiveness of an educational program for pain management in patients with hemophilia-related art…
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CLINICAL_TRIALS research · 2026-02-19Clinical Trial Update: An Observational Cohort Study to Characterize the Effectiveness and Safety of HEMGENIX® in Patients With Hemophilia B
An observational cohort study is being conducted to characterize the effectiveness and safety of Hemgenix in patients with Hemophilia B.
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CLINICAL_TRIALS research · 2026-02-18Clinical Trial Update: SAFE Study: Safety of aPCC Following Emicizumab Prophylaxis [Phase 3]
Phase 3 clinical trial assessing the safety of activated prothrombin complex concentrate after emicizumab prophylaxis in people with Hemophi…
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CLINICAL_TRIALS research · 2026-02-18Clinical Trial Update: Pharmacokinetic Comparison of Efanesoctocog Alfa vs Other EHL-rFVIII Products in Participants With Severe Haemophilia A [Phase 1]
Phase 1 pharmacokinetic comparison of efanesoctocog alfa versus other extended-half-life recombinant FVIII products in participants with sev…
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CLINICAL_TRIALS research · 2026-02-17Clinical Trial Update: Hemophilia A Research Program
A University of Washington-sponsored research program for Hemophilia A (severe) is currently recruiting participants to study new approaches…
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CLINICAL_TRIALS research · 2026-02-13Clinical Trial Update: Compassionate Use of Concizumab if You Have Haemophilia
This clinical trial update covers compassionate use of concizumab for individuals with congenital hemophilia.
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CLINICAL_TRIALS research · 2026-02-12Clinical Trial Update: PCC Treatment for Hemophilia Patients With Inhibitor（2022PCC-A） [Phase 4]
Phase 4 clinical trial evaluating Prothrombin Complex Concentrate (PCC) for hemophilia patients with inhibitors; currently recruiting.
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CLINICAL_TRIALS research · 2026-02-12Clinical Trial Update: National Longitudinal Cohort of Hematological Diseases
Recruiting for a national longitudinal cohort study of hematological diseases sponsored by the Institute of Hematology & Blood Diseases Hosp…