Haemophilia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2021-11-26Clinical Trial Update: A Research Study Looking at How a Factor VIII Medicine Called Turoctocog Alfa Pegol (N8-GP) Works in People With Haemophilia A [Phase 3]
Phase 3 trial update for Turoctocog alfa pegol (N8-GP) in Haemophilia A completed with posted results.
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CLINICAL_TRIALS safety_alert · 2021-07-22Clinical Trial Update: Post-Marketing Safety Study Following Long-Term Prophylactic OptivateTreatment in Subjects With Severe Haemophilia A [Phase 4]
Post-marketing safety study update for long-term prophylaxis with Optivate in severe Haemophilia A was terminated; results posted.
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CLINICAL_TRIALS trial_result · 2021-05-10Clinical Trial Update: A Trial Evaluating Efficacy and Safety of Prophylactic Administration of Concizumab in Patients With Severe Haemophilia A Without Inhibitors [Phase 2]
Phase 2 trial evaluating prophylactic Concizumab in patients with severe haemophilia A without inhibitors has completed with posted results.
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CLINICAL_TRIALS trial_result · 2020-11-03Clinical Trial Update: BAY81-8973 Pediatric Safety and Efficacy Trial [Phase 3]
Phase 3 pediatric trial assessing BAY81-8973 for safety and efficacy in Haemophilia A has completed with results posted.
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CLINICAL_TRIALS trial_result · 2020-07-07Clinical Trial Update: Evaluation of Safety Following Immune Tolerance Induction Treatment With Turoctocog Alfa in Patients With Haemophilia A Following Inhibitor Development in NN7170-4213 Trial [Phase 3]
Phase 3 trial update evaluating safety of immune tolerance induction with turoctocog alfa in Haemophilia A patients with inhibitors; study t…
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CLINICAL_TRIALS trial_result · 2020-04-20Clinical Trial Update: Evaluation of Safety and Efficacy, Including Pharmacokinetics, of NNC 0129-0000-1003 When Administered for Treatment and Prophylaxis of Bleeding in Subjects With Haemophilia A [Phase 3]
Phase 3 trial evaluating safety, efficacy, and pharmacokinetics of NNC 0129-0000-1003 for treatment and prophylaxis in Haemophilia A; study …
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CLINICAL_TRIALS trial_result · 2020-03-18Clinical Trial Update: Research Study to Look at Side Effects During Regular Injection With Factor VIII Medicine Named Turoctocog Alfa for a 8 Weeks Period [Phase 4]
Phase 4 study assessing side effects during regular injections of Turoctocog alfa (Factor VIII) over 8 weeks in people with Haemophilia A.
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CLINICAL_TRIALS trial_result · 2020-01-21Clinical Trial Update: Evaluating the Haemostatic Effect of NNC 0129-0000-1003 During Surgical Procedures in Subjects With Haemophilia A. [Phase 3]
Phase 3 trial evaluating the haemostatic effect of NNC 0129-0000-1003 during surgical procedures in patients with haemophilia A.
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CLINICAL_TRIALS trial_result · 2019-10-30Clinical Trial Update: A Multinational, Open-Label, Non-Controlled Trial on Safety, Efficacy and Pharmacokinetics of NNC 0129-0000-1003 in Previously Treated Paediatric Patients With Severe Haemophilia A [Phase 3]
A multinational Phase 3 open-label trial assessed safety, efficacy, and pharmacokinetics of NNC 0129-0000-1003 in previously treated paediat…
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CLINICAL_TRIALS trial_result · 2019-08-26Clinical Trial Update: Efficacy and Safety of Turoctocog Alfa for Prophylaxis and Treatment of Bleeding Episodes in Previously Treated Chinese Patients With Haemophilia A [Phase 3]
Phase 3 trial evaluating Turoctocog Alfa for prophylaxis and treatment of bleeding episodes in previously treated Chinese patients with Haem…
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CLINICAL_TRIALS trial_result · 2019-01-30Clinical Trial Update: Evaluating the Pharmacokinetics of NovoEight® (Turoctocog Alfa) in Relation to BMI in Subjects With Haemophilia A [Phase 1]
Phase 1 clinical trial completion evaluating how NovoEight (turoctog alfa) pharmacokinetics relate to BMI in individuals with Haemophilia A.
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EMA guidance · 2018-11-30Data from patient registries to replace clinical trials in previously untreated haemophilia patients
EMA discusses using data from patient registries as a potential alternative to traditional clinical trials for previously untreated haemophi…
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CLINICAL_TRIALS trial_result · 2018-10-30Clinical Trial Update: Safety and Efficacy of Turoctocog Alfa in Prevention and Treatment of Bleeds in Previously Untreated Children With Haemophilia A [Phase 3]
Phase 3 trial assessing safety and efficacy of Turoctocog alfa for prevention and treatment of bleeds in previously untreated children with …
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CLINICAL_TRIALS trial_result · 2018-05-09Clinical Trial Update: Safety and Efficacy of NNC-0156-0000-0009 After Long-Term Exposure in Patients With Haemophilia B: An Extension to Trials NN7999-3747 and NN7999-3773 [Phase 3]
A Phase 3 extension study reports on long-term safety and efficacy of NNC-0156-0000-0009 in patients with Haemophilia B, supplementing NN799…
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CLINICAL_TRIALS trial_result · 2018-02-23Clinical Trial Update: Efficacy and Cost Effectiveness of Pharmacokinetic Dosing in Haemophilia A [Phase 4]
Phase 4 trial update evaluating efficacy and cost effectiveness of pharmacokinetic dosing in severe Haemophilia A.
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CLINICAL_TRIALS trial_result · 2018-02-22Clinical Trial Update: An Open-study to Investigate the Safety and Efficacy of Replenine®-VF in Haemophilia B Subjects Undergoing Surgery [Phase 3]
Phase 3 open-study assessing safety and efficacy of Replenine-VF in haemophilia B patients undergoing surgery has completed.
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CLINICAL_TRIALS trial_result · 2018-02-22Clinical Trial Update: A Study to Investigate the Safety and Efficacy of Replenine®-VF in Haemophilia B Patients Undergoing Major Surgery. [Phase 3]
Phase 3 trial update for Replenine-VF in haemophilia B patients undergoing major surgery; study completed.
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CLINICAL_TRIALS trial_result · 2018-02-22Clinical Trial Update: An Open Study to Investigate the Safety and Efficacy of Replenine®-VF in Severe Haemophilia B Patients [Phase 3]
Phase 3 trial investigating safety and efficacy of Replenine-VF in severe Haemophilia B has completed.
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CLINICAL_TRIALS trial_result · 2018-02-15Clinical Trial Update: An Open Study to Investigate the Safety and Efficacy of Optivate® in Severe Haemophilia A Patients. [Phase 3]
A Phase 3 open study assessing the safety and efficacy of Optivate in patients with severe Haemophilia A has completed.
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CLINICAL_TRIALS trial_result · 2018-02-15Clinical Trial Update: A Study to Investigate the Safety and Efficacy of Optivate® in Children Under 6 Years of Age With Haemophilia A. [Phase 3]
Phase 3 trial update assessing safety and efficacy of Optivate® in children under 6 with Haemophilia A has completed.
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CLINICAL_TRIALS trial_result · 2018-02-15Clinical Trial Update: An Open Study to Investigate the Safety and Efficacy of Optivate® in Haemophilia A Patients Undergoing Surgery. [Phase 3]
Phase 3 open study assessing safety and efficacy of Optivate in haemophilia A patients undergoing surgery has completed.
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CLINICAL_TRIALS trial_result · 2018-01-30Clinical Trial Update: Assess the Safety and Efficacy of Individually Tailored Prophylaxis With Human-cl rhFVIII in Patients With Severe Haemophilia A [Phase 3]
Phase 3 trial assessing safety and efficacy of individually tailored prophylaxis with human-cl rhFVIII for severe haemophilia A has complete…
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EMA approval · 2018-01-26First-in-class medicine to prevent bleeding in haemophilia A patients with inhibitors
EMA announces a first-in-class medicine that prevents bleeding in patients with haemophilia A who have inhibitors.
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CLINICAL_TRIALS trial_result · 2017-11-17Clinical Trial Update: Safety, Efficacy and Pharmacokinetics of NNC-0156-0000-0009 in Previously Treated Children With Haemophilia B. [Phase 3]
A Phase 3 trial evaluating the safety, efficacy and pharmacokinetics of NNC-0156-0000-0009 in previously treated children with Haemophilia B…
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CLINICAL_TRIALS trial_result · 2017-08-28Clinical Trial Update: Combining Registry Data in Haemophilia: TARGET H
A completed registry-based study in haemophilia under the TARGET H program, evaluating methods to combine registry data.