Haemophilia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-04-20Clinical Trial Update: Study to Provide Continued Access to Treatment for Patients Completing a Previous Trial With Efanesoctocog Alfa [Phase 3]
A Phase 3 study update describes continued access to efanesoctocog alfa for patients who completed a prior trial.
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CLINICAL_TRIALS research · 2026-04-07Clinical Trial Update: A Research Study Looking at Long-term Treatment With Mim8 in People With Haemophilia A (FRONTIER 4) [Phase 3]
This clinical trial update describes a Phase 3 study (FRONTIER 4) evaluating long-term treatment with Mim8 in people with Haemophilia A, inc…
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CLINICAL_TRIALS research · 2026-02-18Clinical Trial Update: Determinants and Consequences of the Transition to Adulthood for Adolescents With Severe Haemophilia: TRANSHEMO 2, an Ancillary Study to the TRANSHEMO Project
This ancillary study examines the determinants and consequences of transitioning to adulthood for adolescents with severe haemophilia. The s…
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CLINICAL_TRIALS research · 2026-02-13Clinical Trial Update: Study for Turoctocog Alfa Treatment Regimen in Iraqi Haemophilia A Patients
This trial update outlines a study of Turoctocog alfa treatment regimens for Iraqi Haemophilia A patients, and the study is currently recrui…
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CLINICAL_TRIALS research · 2025-12-31Clinical Trial Update: A Research Study Looking at How Food Intake Affects Inno8 in the Body of Healthy People [Phase 1]
A Phase 1 trial sponsored by Novo Nordisk A/S investigates how food intake affects Inno8 in healthy participants, with Haemophilia A listed …
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CLINICAL_TRIALS trial_result · 2025-12-19Clinical Trial Update: A Research Study Investigating Mim8 in People With Haemophilia A [Phase 2]
Phase 2 clinical trial update for Mim8 in Haemophilia A indicates the study has completed.
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CLINICAL_TRIALS research · 2025-12-19Clinical Trial Update: A Study to Investigate the Course of Synovial Hypertrophy in Patients With Haemophilia A on Efanesoctocog Alfa Prophylaxis [Phase 4]
ClinicalTrials.gov study evaluating the progression of synovial hypertrophy in Haemophilia A patients on efanesoctocog alfa prophylaxis (Pha…
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CLINICAL_TRIALS trial_result · 2025-12-08Clinical Trial Update: A Research Study Looking at How Safe it is to Switch From Emicizumab to Mim8 in People With Haemophilia A (FRONTIER 5) [Phase 3]
A Phase 3 trial FRONTER 5 completed, evaluating the safety of switching from emicizumab to Mim8 in people with Haemophilia A, including thos…
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CLINICAL_TRIALS trial_result · 2025-11-10Clinical Trial Update: Efficacy, Safety & Utilisation of Nuwiq, Octanate and Wilate in Previously Untreated & Minimally Treated Haemophilia A Patients
Clinical trial update examining the efficacy, safety, and use of Nuwiq, Octanate, and Wilate in previously untreated and minimally treated H…
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CLINICAL_TRIALS research · 2025-10-24Clinical Trial Update: Defeat Rare Disease in Asia and Pacific (APAC) DRDA - Haemophilia
This clinical trial update notes a Novo Nordisk haemophilia study in the Asia-Pacific region that is currently enrolling by invitation.
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CLINICAL_TRIALS trial_result · 2025-10-14Clinical Trial Update: A Study to Compare the Blood Levels of Mim8 in Healthy Men When Administered With the DV3407-C1 Pen Injector or a Syringe and Cartridge [Phase 1]
This Phase 1 study compares the blood levels of Mim8 in healthy men when administered using the DV3407-C1 Pen Injector versus a syringe and …
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CLINICAL_TRIALS trial_result · 2025-08-29Clinical Trial Update: Post-Marketing Surveillance (Use-results Surveillance) With Esperoct®
Post-marketing surveillance update reporting completion of a use-results study of Esperoct (turoctocog alfa pegol) in patients with Haemophi…
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CLINICAL_TRIALS other · 2025-08-29Clinical Trial Update: Post-Marketing Surveillance (All Case Surveillance) on Treatment With Alhemo® in Patients With Haemophilia A or Haemophilia B With Inhibitors
Post-marketing surveillance trial update for Alhemo® in patients with Haemophilia A or Haemophilia B with inhibitors; the study is currently…
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CLINICAL_TRIALS research · 2025-06-02Clinical Trial Update: Adverse Event Data Collection From External Registries on Nonacog Beta Pegol
This clinical trial update discusses adverse event data collection from external registries for nonacog beta pegol in haemophilia B, with th…
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CLINICAL_TRIALS trial_result · 2025-04-10Clinical Trial Update: Gene Therapy Study in Severe Haemophilia A Patients (270-201) [Phase 1, Phase 2]
A Phase 1/2 gene therapy trial (NCT02576795) evaluating valoctocogene roxaparvovec for severe haemophilia A has completed, with results post…
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CLINICAL_TRIALS trial_result · 2025-01-08Clinical Trial Update: Register of Patients With haEmophilia A tReated With Afstyla®
A patient registry for Haemophilia A patients treated with Afstyla has completed.
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CLINICAL_TRIALS research · 2025-01-08Clinical Trial Update: Observatory of Patients With Haemophilia B Treated by IdElvion®
Observational registry of patients with haemophilia B treated with IdElvion, currently active and not recruiting.
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CLINICAL_TRIALS trial_result · 2024-10-31Clinical Trial Update: Safety and Efficacy of Turoctocog Alfa Pegol (N8-GP) in Previously Untreated Patients With Haemophilia A [Phase 3]
Phase 3 trial evaluating the safety and efficacy of Turoctocog alfa pegol (N8-GP) in previously untreated patients with Haemophilia A; resul…
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CLINICAL_TRIALS trial_result · 2024-10-02Clinical Trial Update: A Study to Evaluate the Real-world Usage and Effectiveness of Elocta and Alprolix in Patients With Haemophilia A or B
Completed study evaluating real-world usage and effectiveness of Elocta and Alprolix in patients with Haemophilia A or B.
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CLINICAL_TRIALS research · 2024-08-30Clinical Trial Update: Virtual Evaluations of Joint Health Using Wearable Sensors in Persons With Haemophilia (VESPA)
This clinical trial evaluates virtual joint-health assessments in people with haemophilia using wearable sensors; the study status is curren…
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CLINICAL_TRIALS trial_result · 2024-07-12Clinical Trial Update: An Observational Study to Evaluate Physical Activity, Bleeding Incidence and Health Related Quality of Life, in Participants With Haemophilia A Without Inhibitors Receiving Standard of Care Treatment
A completed observational study in people with Haemophilia A without inhibitors evaluating physical activity, bleeding incidence, and health…
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EMA guidance · 2024-05-31New gene therapy treatment for haemophilia B
The EMA announced that the gene therapy Durveqtix for haemophilia B has received PRIME designation to support its development and potential …
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CLINICAL_TRIALS trial_result · 2024-01-18Clinical Trial Update: Efficacy and Safety of Turoctocog Alfa Pegol (N8-GP) for Prophylaxis and Treatment of Bleeding Episodes in Previously Treated Chinese Patients With Haemophilia A (pathfinder10) [Phase 3]
Phase 3 study evaluating the efficacy and safety of N8-GP (turoctocog alfa pegol) for prophylaxis and treatment of bleeding episodes in prev…
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CLINICAL_TRIALS trial_result · 2023-12-29Clinical Trial Update: Safety and Efficacy of Nonacog Beta Pegol (N9-GP) in Previously Untreated Patients With Haemophilia B [Phase 3]
Phase 3 trial evaluating the safety and efficacy of Nonacog Beta Pegol (N9-GP) in previously untreated patients with Haemophilia B; results …
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EMA approval · 2022-12-16First gene therapy to treat haemophilia B
The European Medicines Agency approved the first gene therapy designed to treat haemophilia B, marking a milestone in genetic treatment for …