EMA
guidance
· 2024-05-31
New gene therapy treatment for haemophilia B
Summary
The EMA announced that the gene therapy Durveqtix for haemophilia B has received PRIME designation to support its development and potential to improve patients'…
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Diseases / indications
Drugs mentioned
Snippet
Durveqtix received support through the PRIority Medicines (PRIME) scheme due to its potential to improve patients’ quality of life