Glycogenosis 2

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CLINICAL_TRIALS trial_result · 2014-02-05
Clinical Trial Update: A Study of the Safety and Pharmacokinetics of rhGAA in Siblings With Glycogen Storage Disease Type II [Phase 2]
Phase 2 study evaluating the safety and pharmacokinetics of recombinant human acid alpha-glucosidase (rhGAA) in siblings with glycogen stora…