CLINICAL_TRIALS ClinicalTrials.gov record update

Open-Label, Pilot Study of the Safety, Pharmacokinetics and Pharmacodynamics of Recombinant Human Acid Alpha-Glucosidase (rhGAA) as Enzyme Replacement Therapy in Siblings With Glycogen Storage Disease Type II (GSD-II).

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Record identity and dates

Source: ClinicalTrials.gov
Source record ID: NCT00051935
Title field or adapter rule: protocolSection.identificationModule.officialTitle
Ingested At: 2026-04-28T10:35:33.539895+00:00
Published At: 2014-02-05T00:00:00+00:00
Record Updated At: 2014-02-05
Timestamp Basis: source retrieval time was not retained by the feed adapter
Date limitation: source retrieval time was not retained by the feed adapter

protocolSection.conditionsModule.conditions: ["Glycogen Storage Disease Type II", "Pompe Disease", "Acid Maltase Deficiency Disease", "Glycogenosis 2"]
protocolSection.statusModule.lastUpdatePostDateStruct.date: "2014-02-05"
protocolSection.identificationModule.nctId: "NCT00051935"
protocolSection.identificationModule.officialTitle: "Open-Label, Pilot Study of the Safety, Pharmacokinetics and Pharmacodynamics of Recombinant Human Acid Alpha-Glucosidase (rhGAA) as Enzyme Replacement Therapy in Siblings With Glycogen Storage Disease Type II (GSD-II)."
protocolSection.statusModule.overallStatus: "COMPLETED"
protocolSection.designModule.phases: ["PHASE2"]
protocolSection.statusModule.resultsFirstPostDateStruct.date: ""

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