Glycogen Storage Disease Type
📧 Sign up to get email alerts when something new happens for Glycogen Storage Disease Type.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2026-03-18Clinical Trial Update: Study of Long-Term Safety and Efficacy on Gene Therapy in Glycogen Storage Disease Type Ia
Completed study reporting long-term safety and efficacy data for a gene therapy in Glycogen storage disease type I (GSD Ia) with results pos…
-
CLINICAL_TRIALS trial_result · 2026-03-10Clinical Trial Update: Accuracy of Home Lactate Meter and Accu-chek Glucometer in Patients With Glycogen Storage Disease
A clinical trial evaluating the accuracy of home lactate meters and Accu-chek glucometers in patients with glycogen storage disease, current…
-
CLINICAL_TRIALS trial_result · 2025-09-04Clinical Trial Update: Triheptanoin in Mc Ardle [Phase 2]
This clinical trial update reports the completion of a Phase 2 study of triheptanoin for Glycogen Storage Disease Type V (McArdle disease) i…
-
CLINICAL_TRIALS trial_result · 2019-10-28Clinical Trial Update: Safety, Efficacy Evaluation of Empagliflozin Administration for Neutropenia in Glycogenosis Type 1b and G6PC3 Deficiency [Phase 2]
Phase 2 clinical trial evaluating safety and efficacy of empagliflozin for neutropenia in glycogen storage disease Type I (GSD I) due to G6P…
-
CLINICAL_TRIALS trial_result · 2019-10-16Clinical Trial Update: The Effect of Triheptanoin in Adults With McArdle Disease (Glycogen Storage Disease Type V) [Phase 2]
Phase 2 trial examining the effects of triheptanoin in adults with McArdle disease (Glycogen Storage Disease Type V) has completed.
- Want full summaries, importance scores, and drug timelines? Upgrade to Plus or Pro.
-
CLINICAL_TRIALS trial_result · 2018-02-05Clinical Trial Update: Sodium Valproate for GSDV [Phase 2]
Phase 2 clinical trial update for sodium valproate in Glycogen Storage Disease Type V (McArdle Disease) has completed.
-
CLINICAL_TRIALS trial_result · 2017-08-03Clinical Trial Update: Comparison of the Effect of a Novel Starch (Glycosade) Versus Gastrostomy Tube-Dextrose Infusion on Overnight Euglycaemia Control in Children With Glycogen Storage Disease Type I: Open Label Demonstration Trial [NA]
Open-label demonstration trial comparing Glycosade (cornstarch) to gastrostomy tube–dextrose infusion for overnight euglycemia control in ch…
-
CLINICAL_TRIALS trial_result · 2015-09-25Clinical Trial Update: Sleep and Quality of Life in Patients With Glycogen Storage Disease on Standard Versus Modified Uncooked Cornstarch
A completed clinical trial comparing sleep and quality of life in patients with glycogen storage disease on standard versus modified uncooke…