Glycogen Storage Disease Type
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2026-03-18Clinical Trial Update: Study of Long-Term Safety and Efficacy on Gene Therapy in Glycogen Storage Disease Type Ia
Completed study reporting long-term safety and efficacy data for a gene therapy in Glycogen storage disease type I (GSD Ia) with results pos…
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CLINICAL_TRIALS trial_result · 2026-03-10Clinical Trial Update: Accuracy of Home Lactate Meter and Accu-chek Glucometer in Patients With Glycogen Storage Disease
A clinical trial evaluating the accuracy of home lactate meters and Accu-chek glucometers in patients with glycogen storage disease, current…
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CLINICAL_TRIALS research · 2025-12-15Clinical Trial Update: A Study of mRNA-3745 in Adult and Pediatric Participants With Glycogen Storage Disease Type 1a (GSD1a) [Phase 1, Phase 2]
A Phase 1/2 clinical trial evaluating mRNA-3745 for Glycogen storage disease type I (Ia) is ongoing, with the study conducted by Moderna and…
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CLINICAL_TRIALS trial_result · 2025-09-04Clinical Trial Update: Triheptanoin in Mc Ardle [Phase 2]
This clinical trial update reports the completion of a Phase 2 study of triheptanoin for Glycogen Storage Disease Type V (McArdle disease) i…
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CLINICAL_TRIALS research · 2025-08-11Clinical Trial Update: Carbon-13 Magnetic Resonance Spectroscopy in Glycogen Storage Diseases
This update describes a clinical study using carbon-13 magnetic resonance spectroscopy to investigate glycogen storage diseases, including M…
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CLINICAL_TRIALS research · 2025-04-24Clinical Trial Update: Dietary Treatment Strategies and Metabolic Control in Glycogen Storage Disease Type I [NA]
A clinical trial update on dietary treatment strategies to improve metabolic control in glycogen storage disease type I, currently recruitin…
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CLINICAL_TRIALS trial_result · 2019-10-28Clinical Trial Update: Safety, Efficacy Evaluation of Empagliflozin Administration for Neutropenia in Glycogenosis Type 1b and G6PC3 Deficiency [Phase 2]
Phase 2 clinical trial evaluating safety and efficacy of empagliflozin for neutropenia in glycogen storage disease Type I (GSD I) due to G6P…
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CLINICAL_TRIALS trial_result · 2019-10-16Clinical Trial Update: The Effect of Triheptanoin in Adults With McArdle Disease (Glycogen Storage Disease Type V) [Phase 2]
Phase 2 trial examining the effects of triheptanoin in adults with McArdle disease (Glycogen Storage Disease Type V) has completed.
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CLINICAL_TRIALS trial_result · 2018-02-05Clinical Trial Update: Sodium Valproate for GSDV [Phase 2]
Phase 2 clinical trial update for sodium valproate in Glycogen Storage Disease Type V (McArdle Disease) has completed.
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CLINICAL_TRIALS trial_result · 2017-08-03Clinical Trial Update: Comparison of the Effect of a Novel Starch (Glycosade) Versus Gastrostomy Tube-Dextrose Infusion on Overnight Euglycaemia Control in Children With Glycogen Storage Disease Type I: Open Label Demonstration Trial [NA]
Open-label demonstration trial comparing Glycosade (cornstarch) to gastrostomy tube–dextrose infusion for overnight euglycemia control in ch…
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CLINICAL_TRIALS trial_result · 2015-09-25Clinical Trial Update: Sleep and Quality of Life in Patients With Glycogen Storage Disease on Standard Versus Modified Uncooked Cornstarch
A completed clinical trial comparing sleep and quality of life in patients with glycogen storage disease on standard versus modified uncooke…
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CLINICAL_TRIALS research · 2015-03-23Clinical Trial Update: Overnight Feeding Study in Glycogen Storage Disease Type 1 [NA]
The University of Zurich-conducted overnight feeding study in patients with glycogen storage disease type I has completed.