Friedreich Ataxia
📧 Sign up to get email alerts when something new happens for Friedreich Ataxia.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2019-12-19Clinical Trial Update: Efficacy, Tolerability, and Pharmacokinetics of Multiple Doses of Oral TAK-831 in Adults With Friedreich Ataxia [Phase 2]
Phase 2 trial updates on multiple-dose oral TAK-831 in adults with Friedreich Ataxia, reporting efficacy, tolerability, and pharmacokinetics…
-
CLINICAL_TRIALS trial_result · 2019-12-05Clinical Trial Update: (+) Epicatechin to Treat Friedreich's Ataxia [Phase 2]
Phase 2 trial investigating epicatechin for Friedreich's ataxia has completed with results posted.
-
CLINICAL_TRIALS trial_result · 2019-06-28Clinical Trial Update: Rehabilitative Trial With Cerebello-Spinal tDCS in Neurodegenerative Ataxia [NA]
Clinical trial update for a rehabilitative tDCS approach in various cerebellar ataxias, status completed with results posted in 2019.
-
CLINICAL_TRIALS trial_result · 2019-03-18Clinical Trial Update: Idebenone to Treat Friedreich's Ataxia [Phase 2]
Phase 2 clinical trial update for idebenone in Friedreich's ataxia is completed.
-
CLINICAL_TRIALS trial_result · 2018-05-18Clinical Trial Update: Safety, Tolerability and Efficacy of ACTIMMUNE® Dose Escalation in Friedreich's Ataxia Study [Phase 3]
Phase 3 trial update evaluating safety, tolerability and efficacy of ACTIMMUNE (interferon gamma-1b) in Friedreich's Ataxia; results posted …
- Want full summaries, importance scores, and drug timelines? Upgrade to Plus or Pro.
-
CLINICAL_TRIALS trial_result · 2018-05-01Clinical Trial Update: Long-Term Safety Extension Study of ACTIMMUNE® (Interferon γ-1b) in Children and Young Adults With Friedreich's Ataxia [Phase 3]
Long-term safety data from a safety-extension study of interferon gamma-1b (ACTIMMUNE) in children and young adults with Friedreich's Ataxia…
-
CLINICAL_TRIALS trial_result · 2018-03-05Clinical Trial Update: Long-Term Safety and Tolerability of Idebenone in Friedreich's Ataxia Patients (MICONOS Extension) [Phase 3]
The document reports long-term safety and tolerability data from the Phase 3 extension study (MICONOS Extension) of idebenone in Friedreich'…
-
CLINICAL_TRIALS trial_result · 2017-12-08Clinical Trial Update: Safety, Tolerability and Efficacy of ACTIMMUNE® Dose Escalation in Friedreich's Ataxia [Phase 3]
Phase 3 study evaluating dose escalation of ACTIMMUNE for Friedreich's Ataxia reported safety, tolerability, and efficacy results; the trial…
-
CLINICAL_TRIALS trial_result · 2017-07-02Clinical Trial Update: Effect of Nicotinamide in Friedreich's Ataxia [Phase 2]
Nicotinamide is being studied in a Phase 2 trial for Friedreich's ataxia, with the trial status listed as unknown.
-
CLINICAL_TRIALS trial_result · 2017-04-21Clinical Trial Update: A Phase IIa Trial to Test Safety and Efficacy Interferon Gamma Treatment in Elevating Frataxin Levels in FRDA Patients [Phase 2]
A Phase IIa trial evaluating whether interferon gamma-1b can safely elevate frataxin levels in Friedreich's ataxia has completed.
-
CLINICAL_TRIALS trial_result · 2016-11-08Clinical Trial Update: Safety Study of Carbamylated Erythropoietin to Treat Patients With the Neurodegenerative Disorder Friedreich's Ataxia [Phase 2]
A Phase 2 safety study of carbamylated erythropoietin in patients with Friedreich's ataxia has completed.
-
CLINICAL_TRIALS trial_result · 2016-10-06Clinical Trial Update: Safety and Pharmacology Study of VP 20629 in Adults With Friedreich's Ataxia [Phase 1]
Phase 1 safety and pharmacology study of VP 20629 in adults with Friedreich's Ataxia has been completed with results posted.
-
CLINICAL_TRIALS trial_result · 2016-09-19Clinical Trial Update: An Objective Double-blind Evaluation of Bupropion and Citalopram in an Individual With Friedreich Ataxia [Phase 4]
A Phase 4, double-blind evaluation of bupropion and citalopram was conducted in a single patient with Friedreich ataxia, with results posted…
-
CLINICAL_TRIALS trial_result · 2016-06-29Clinical Trial Update: EPI-743 in Friedreich's Ataxia Point Mutations [Phase 2]
Phase 2 trial of EPI-743 for Friedreich's Ataxia with point mutations has completed.
-
CLINICAL_TRIALS trial_result · 2016-06-27Clinical Trial Update: A Study of Efficacy, Safety and Tolerability of Idebenone in the Treatment of Friedreich's Ataxia (FRDA) Patients [Phase 3]
Phase 3 study assessing the efficacy, safety and tolerability of idebenone in Friedreich's ataxia has completed, with results posted in 2016…
-
CLINICAL_TRIALS trial_result · 2016-03-09Clinical Trial Update: Patient Reported Outcomes in Friedreich's Ataxia Patients After Withdrawal From Treatment With Idebenone (PROTI) [Phase 3]
This Phase 3 trial update summarizes patient-reported outcomes in Friedreich's Ataxia patients after withdrawal from idebenone treatment. Th…
-
CLINICAL_TRIALS trial_result · 2015-08-11Clinical Trial Update: Efficacy Study of Epoetin Alfa in Friedreich Ataxia [Phase 2]
Phase 2 efficacy study evaluating epoetin alfa in Friedreich Ataxia has completed.
-
CLINICAL_TRIALS trial_result · 2015-04-30Clinical Trial Update: Interferon Gamma-1b in Friedreich Ataxia (FRDA) [Phase 2]
Phase 2 trial of Interferon Gamma-1b in Friedreich Ataxia completed; results posted in 2015.
-
CLINICAL_TRIALS trial_result · 2014-01-22Clinical Trial Update: A Study of Resveratrol as Treatment for Friedreich Ataxia [Phase 1, Phase 2]
A Phase 1/2 clinical trial evaluating resveratrol for Friedreich Ataxia has completed. The study was sponsored by Murdoch Children's Researc…
-
CLINICAL_TRIALS trial_result · 2013-09-04Clinical Trial Update: Effect of Pioglitazone Administered to Patients With Friedreich's Ataxia: Proof of Concept [Phase 3]
A Phase 3 trial of pioglitazone in Friedreich's ataxia has been completed. The study provides a proof-of-concept for this approach.
-
CLINICAL_TRIALS trial_result · 2013-05-21Clinical Trial Update: Efficacy of EGb761 in Patients Suffering From Friedreich Ataxia [Phase 2]
A Phase 2 trial evaluating EGb761 for Friedreich Ataxia has completed with posted results.
-
CLINICAL_TRIALS trial_result · 2012-07-24Clinical Trial Update: Pilot Study of Varenicline (Chantix®) in the Treatment of Friedreich's Ataxia [Phase 2, Phase 3]
The phase 2/3 pilot trial of varenicline (Chantix) for Friedreich's Ataxia was terminated.
-
CLINICAL_TRIALS trial_result · 2011-12-29Clinical Trial Update: Study to Assess the Efficacy, Safety and Tolerability of Idebenone in the Treatment of Friedreich's Ataxia [Phase 3]
Phase 3 trial assessing idebenone for Friedreich's ataxia completed with posted results.
-
CLINICAL_TRIALS trial_result · 2011-08-04Clinical Trial Update: Study to Assess the Safety and Tolerability of Idebenone in the Treatment of Friedreich's Ataxia Patients [Phase 3]
Phase 3 trial update on idebenone for Friedreich's ataxia; study completed with results posted in 2011.
-
CLINICAL_TRIALS trial_result · 2011-06-27Clinical Trial Update: A Study Investigating the Long-term Safety and Efficacy of Deferiprone in Patients With Friedreich's Ataxia [Phase 2]
This document reports the completion of a Phase 2 study evaluating the long-term safety and efficacy of deferiprone in patients with Friedre…