Fragile Syndrome
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2026-02-27Clinical Trial Update: A Study to Investigate the Effects and Safety of SPG601 for the Treatment of Fragile X Syndrome in Male Participants [Phase 2, Phase 3]
This clinical trial update describes SPG601 being studied for Fragile X syndrome in male participants, currently in Phase 2/3 and not yet re…
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CLINICAL_TRIALS trial_result · 2026-02-04Clinical Trial Update: A Randomized Study of BPN14770 in Male Adolescents (Aged 9 to < 18 Years) With Fragile X Syndrome [Phase 2, Phase 3]
A randomized Phase 2/3 trial of BPN14770 in male adolescents aged 9 to under 18 with Fragile X syndrome has completed.
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CLINICAL_TRIALS trial_result · 2026-01-08Clinical Trial Update: A Trial of Metformin in Individuals With Fragile X Syndrome (Met) [Phase 2]
Phase 2 trial evaluating metformin in individuals with Fragile X syndrome has completed; this entry provides a status update.
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CLINICAL_TRIALS trial_result · 2025-12-31Clinical Trial Update: Glutaminergic Transmission in Autism : Molecular Imaging Exploration [Phase 1]
A Phase 1 clinical trial investigating glutamatergic transmission in autism and Fragile X syndrome has completed.
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CLINICAL_TRIALS trial_result · 2025-12-23Clinical Trial Update: Placebo-Controlled, Single-Dose Challenge Study of Gaboxadol in Adult Males With Fragile X Syndrome (FXS) [Phase 2]
A Phase 2, placebo-controlled, single-dose trial of gaboxadol in adult males with Fragile X syndrome has completed.
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CLINICAL_TRIALS trial_result · 2025-12-17Clinical Trial Update: Clinical Study of Cannabidiol in Children, Adolescents, and Young Adults With Fragile X Syndrome [Phase 3]
This update covers a Phase 3 clinical trial evaluating cannabidiol for Fragile X Syndrome in children, adolescents, and young adults, with t…
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CLINICAL_TRIALS trial_result · 2025-12-02Clinical Trial Update: Pediatric Patients With Metabolic or Other Genetic Disorders
This clinical trial update reports the completion of a pediatric study examining metabolic or other genetic disorders, including Autism Spec…
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CLINICAL_TRIALS trial_result · 2025-11-05Clinical Trial Update: Open Label Extension to Assess the Long-Term Safety and Tolerability of ZYN002 in Children and Adolescents With FXS [Phase 2, Phase 3]
Open-label extension study to evaluate the long-term safety and tolerability of ZYN002 (cannabidiol) in children and adolescents with Fragil…
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CLINICAL_TRIALS trial_result · 2025-07-23Clinical Trial Update: A Study of BPN14770 in Male Adults (Aged 18 to 45) With Fragile X Syndrome [Phase 3]
A Phase 3 trial of BPN14770 in adult males with Fragile X Syndrome has completed.
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CLINICAL_TRIALS trial_result · 2025-05-04Clinical Trial Update: Neural Biomarkers in Fragile X Syndrome
A completed clinical trial by Connecta Therapeutics investigating neural biomarkers in Fragile X syndrome.
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CLINICAL_TRIALS trial_result · 2025-01-23Clinical Trial Update: CTH120 First-in-Human Study: Single and Multiple Ascending Doses and Potential Food Interaction [Phase 1]
Connecta Therapeutics reports the completion of its first-in-human Phase 1 study of CTH120 in Fragile X Syndrome, evaluating single and mult…
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CLINICAL_TRIALS trial_result · 2025-01-17Clinical Trial Update: A Trial of Metformin in Individuals With Fragile X Syndrome [Phase 2, Phase 3]
The document reports the completion of a Phase 2/Phase 3 clinical trial evaluating metformin in individuals with Fragile X syndrome.
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CLINICAL_TRIALS trial_result · 2025-01-14Clinical Trial Update: Study of SPG601 in Adult Men With Fragile X Syndrome [Phase 2]
A Phase 2 study of SPG601 in adult men with Fragile X Syndrome has completed.
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CLINICAL_TRIALS trial_result · 2024-12-19Clinical Trial Update: A 2-Period Crossover Study of BPN14770 in Adults Males With Fragile X Syndrome [Phase 2]
A Phase 2 two-period crossover trial of BPN14770 in adult males with Fragile X Syndrome has completed and results have been posted.
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CLINICAL_TRIALS trial_result · 2024-10-08Clinical Trial Update: Protein Synthesis in the Brain of Patients With Fragile X Syndrome
A completed clinical trial investigated protein synthesis in the brain of patients with Fragile X Syndrome, with healthy volunteers also par…
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CLINICAL_TRIALS trial_result · 2024-09-19Clinical Trial Update: ERG/5-HTP in Fragile X Syndrome (FXS) [Phase 2]
Phase 2 trial update for ERG/5-HTP in Fragile X Syndrome reports completed results with findings posted on 2024-09-19.
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CLINICAL_TRIALS trial_result · 2024-01-23Clinical Trial Update: A Study of OV101 in Individuals With Fragile X Syndrome [Phase 2]
Phase 2 clinical trial of OV101 in Fragile X Syndrome has completed and results were posted in 2024.
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CLINICAL_TRIALS trial_result · 2023-11-09Clinical Trial Update: Effects of Social Gaze Training on Brain and Behavior in Fragile X Syndrome [Phase 1, Phase 2]
A clinical trial evaluating social gaze training on brain and behavior in Fragile X Syndrome (Phase 1/Phase 2) has completed recruitment.
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CLINICAL_TRIALS trial_result · 2023-10-10Clinical Trial Update: AFQ056 for Language Learning in Children With FXS [Phase 2]
Phase 2 trial update for AFQ056 in language learning in children with Fragile X Syndrome has completed with results posted.
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CLINICAL_TRIALS trial_result · 2023-04-10Clinical Trial Update: Ganaxolone Treatment in Children With Fragile X Syndrome [Phase 2]
Phase 2 clinical trial update on ganaxolone for Fragile X Syndrome in children; results posted after completion.
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CLINICAL_TRIALS trial_result · 2022-07-22Clinical Trial Update: Clinical Trial for Asses the Safety and Efficacy of Vitamin C and Vitamin E in Combination Versus Placebo for Treating Cognitive and Behavior Disorder in Children With Fragile X Syndrome [Phase 3]
Phase 3 clinical trial evaluating vitamin C and vitamin E combination vs placebo for cognitive and behavioral disorders in children with Fra…
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CLINICAL_TRIALS trial_result · 2021-11-24Clinical Trial Update: Neurophysiological and Acute Pharmacological Studies in FXS Patients [EARLY_Phase 1]
Early-phase trial exploring neurophysiological and acute pharmacological effects in Fragile X Syndrome; study completed with results posted.
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CLINICAL_TRIALS trial_result · 2021-02-04Clinical Trial Update: Metformin in Children and Adults With Fragile X Syndrome [Phase 2]
Phase 2 clinical trial investigating metformin in children and adults with Fragile X Syndrome has completed.
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CLINICAL_TRIALS trial_result · 2020-12-23Clinical Trial Update: Safety and Efficacy of AFQ056 in Adult Patients With Fragile X Syndrome [Phase 2]
Phase 2 clinical trial update evaluating safety and efficacy of AFQ056 in adults with Fragile X Syndrome.
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CLINICAL_TRIALS trial_result · 2020-02-11Clinical Trial Update: Efficacy, Safety and Tolerability of AFQ056 in Fragile X Patients [Phase 2]
Phase 2 clinical trial update on AFQ056 for Fragile X Syndrome evaluating efficacy, safety, and tolerability.