Familial Dysautonomia
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CLINICAL_TRIALS research · 2026-04-13Clinical Trial Update: Dexmedetomidine Sublingual Film for the Ambulatory Treatment of Hyperadrenergic Autonomic Crisis in Patients With Familial Dysautonomia [Phase 2]
A Phase 2 clinical trial is evaluating a dexmedetomidine sublingual film for ambulatory treatment of hyperadrenergic autonomic crises in pat…
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CLINICAL_TRIALS research · 2025-11-10Clinical Trial Update: The Natural History of Familial Dysautonomia
A natural history study of Familial Dysautonomia (Riley-Day syndrome) is currently recruiting. The study also references related hereditary …