Familial Dysautonomia
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CLINICAL_TRIALS research · 2026-04-13Clinical Trial Update: Dexmedetomidine Sublingual Film for the Ambulatory Treatment of Hyperadrenergic Autonomic Crisis in Patients With Familial Dysautonomia [Phase 2]
A Phase 2 clinical trial is evaluating a dexmedetomidine sublingual film for ambulatory treatment of hyperadrenergic autonomic crises in pat…
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CLINICAL_TRIALS trial_result · 2026-03-04Clinical Trial Update: Pilot Study of Dexmedetomidine Sublingual Film for the Ambulatory Treatment of Hyperadrenergic Autonomic Crisis in Patients With Familial Dysautonomia [Phase 2]
This is an update on a Phase 2 pilot trial of a dexmedetomidine sublingual film for ambulatory treatment of hyperadrenergic autonomic crises…
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CLINICAL_TRIALS research · 2025-11-10Clinical Trial Update: The Natural History of Familial Dysautonomia
A natural history study of Familial Dysautonomia (Riley-Day syndrome) is currently recruiting. The study also references related hereditary …
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CLINICAL_TRIALS trial_result · 2021-02-21Clinical Trial Update: The Nutritional Supplement Phosphatidylserine in Patients With Familial Dysautonomia [Phase 2]
Phase 2 clinical trial assessing phosphatidylserine in patients with familial dysautonomia has completed.
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CLINICAL_TRIALS trial_result · 2019-01-29Clinical Trial Update: A Trial of Cognitive Behavioral Therapy in Familial Dysautonomia [NA]
This entry reports the completion of a clinical trial evaluating cognitive behavioral therapy for familial dysautonomia with co-morbid dysth…
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CLINICAL_TRIALS trial_result · 2017-08-17Clinical Trial Update: Efficacy Study of an Online Educational Module Before Carrier Genetic Screening in Persons of Ashkenazi Jewish Descent. [NA]
Completed efficacy study evaluating an online educational module used before carrier genetic screening in people of Ashkenazi Jewish descent…
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CLINICAL_TRIALS trial_result · 2016-06-02Clinical Trial Update: The Effects Of Bronchodilator Therapy On Respiratory And Autonomic Function In Patients With Familial Dysautonomia [Phase 3]
A Phase 3 clinical trial evaluating bronchodilator therapy for respiratory and autonomic function in patients with familial dysautonomia has…
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CLINICAL_TRIALS trial_result · 2016-03-28Clinical Trial Update: Carbidopa for the Treatment of Nausea and Vomiting in Familial Dysautonomia [Phase 3]
A Phase 3 trial evaluating carbidopa for nausea and vomiting in familial dysautonomia has completed and posted results.