Erythropoietic Protoporphyria

• CLINICAL_TRIALS research · 2025-12-18
  Clinical Trial Update: HELIOS: Open-Label, Long-Term Extension Study to Investigate the Safety, Tolerability, and Efficacy of DISC-1459 (Bitopertin) in Participants With EPP or XLP [Phase 2, Phase 3]

  Open-label HELIOS extension study evaluating DISC-1459 (Bitopertin) for safety, tolerability, and efficacy in erythropoietic protoporphyria …

• CLINICAL_TRIALS research · 2025-12-11
  Clinical Trial Update: Extension Study to Evaluate Safety and Tolerability of Oral Dersimelagon (MT-7117) in Subjects With Erythropoietic Protoporphyria (EPP) or X-Linked Protoporphyria (XLP) [Phase 3]

  An extension study in Phase 3 to evaluate the safety and tolerability of oral dersimelagon (MT-7117) in subjects with erythropoietic protopo…

• CLINICAL_TRIALS research · 2025-05-14
  Clinical Trial Update: GATEWAY: A Phase 2a Study of PORT-77 in Adults With Erythropoietic Protoporphyria [Phase 2]

  A Phase 2a clinical trial update for PORT-77 in adults with erythropoietic protoporphyria, currently enrolling by invitation.

• CLINICAL_TRIALS research · 2020-04-17
  Clinical Trial Update: Erythropoietic Protoporphyrias: Studies of the Natural History, Genotype-Phenotype Correlations, and Psychosocial Impact

  Clinical trial update focusing on natural history, genotype-phenotype correlations, and psychosocial impact in erythropoietic protoporphyria…

• CLINICAL_TRIALS research · 2006-10-11
  Clinical Trial Update: Does Exercise and Heat Increase the Lightsensibility in Patients With Erythropoietic Protoporphyria [NA]

  This clinical trial update investigates whether exercise and heat affect light sensitivity in patients with erythropoietic protoporphyria; t…

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