Erythropoietic Protoporphyria
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CLINICAL_TRIALS trial_result · 2026-08-21Clinical Trial Update: Study of Bitopertin in Participants With EPP or XLP (APOLLO) [Phase 3]
Phase 3 trial ongoing evaluating bitopertin in participants with Erythropoietic Protoporphyria and X-Linked Protoporphyria.
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CLINICAL_TRIALS trial_result · 2026-08-12Clinical Trial Update: Study of Bitopertin in Participants With EPP or XLP (APOLLO) [Phase 3]
Phase 3 clinical trial update for bitopertin in participants with erythropoietic protoporphyria (EPP) and X-linked protoporphyria (XLP).
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CLINICAL_TRIALS trial_result · 2026-08-03Clinical Trial Update: Study of Bitopertin in Participants With EPP or XLP (APOLLO) [Phase 3]
Phase 3 study of bitopertin in participants with erythropoietic protoporphyria (EPP) or X-linked protoporphyria (XLP) is active but not curr…
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CLINICAL_TRIALS trial_result · 2026-07-30Clinical Trial Update: Study of Bitopertin in Participants With EPP or XLP (APOLLO) [Phase 3]
Phase 3 trial update for bitopertin in erythropoietic protoporphyria (EPP) and X-linked protoporphyria (XLP) is active but not recruiting.
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CLINICAL_TRIALS trial_result · 2026-07-27Clinical Trial Results: Pharmacokinetics of Afamelanotide in Erythropoietic Protoporphyria Patients [Phase 1, Phase 2]
Phase 1/2 trial reports pharmacokinetics of afamelanotide in patients with erythropoietic protoporphyria.
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CLINICAL_TRIALS trial_result · 2026-07-08Clinical Trial Update: Study of Bitopertin in Participants With EPP or XLP (APOLLO) [Phase 3]
Phase 3 clinical trial update for bitopertin in patients with Erythropoietic Protoporphyria (EPP) or X-Linked Protoporphyria (XLP).
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CLINICAL_TRIALS trial_result · 2026-06-29Clinical Trial Results: Effect of Oral Cimetidine in the Protoporphyrias [Phase 2]
Phase 2 clinical trial assessing oral cimetidine for protoporphyria showing completed results.
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CLINICAL_TRIALS trial_result · 2026-06-04Clinical Trial Update: Study of Bitopertin in Participants With EPP or XLP (APOLLO) [Phase 3]
Phase 3 clinical trial of bitopertin (APOLLO) in participants with erythropoietic protoporphyria (EPP) or X-linked protoporphyria (XLP) is a…
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CLINICAL_TRIALS trial_result · 2026-06-04Clinical Trial Update: INcreased Sun Exposure Without Pain In Research Participants With EPP or XLP [Phase 3]
Phase 3 trial examining increased sun exposure without pain in participants with Erythropoietic Protoporphyria (EPP) or X-Linked Protoporphy…
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CLINICAL_TRIALS other · 2026-04-13Clinical Trial Update: Study of Bitopertin in Participants With EPP or XLP (APOLLO) [Phase 3]
Phase 3 APOLLO trial evaluating bitopertin in Erythropoietic Protoporphyria and X-Linked Protoporphyria is currently active but not recruiti…
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CLINICAL_TRIALS trial_result · 2026-03-25Clinical Trial Update: Pharmacokinetics of Afamelanotide in Erythropoietic Protoporphyria Patients [Phase 1, Phase 2]
The study reports pharmacokinetics of afamelanotide in erythropoietic protoporphyria patients across Phase 1 and Phase 2, providing PK data …
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EMA approval · 2026-01-30EMA Authorised: Scenesse (afamelanotide) — Clinuvel Europe Limited
The EMA authorised Scenesse (afamelanotide) for erythropoietic protoporphyria, with Clinuvel Europe Limited as the marketing authorisation h…
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CLINICAL_TRIALS withdrawal · 2026-01-29Clinical Trial Update: Effect of Bitopertin on the Liver and on Levels of Protoporphyrin IX in Bile, Blood, Liver, and Stool in Patients With Erythropoietic Protoporphyria/X-linked Protoporphyria and Increased Liver Stiffness and/or Liver Enzymes at Baseline [Phase 1]
A Phase 1 clinical trial evaluating Bitopertin in patients with erythropoietic protoporphyria or X-linked protoporphyria and baseline liver …
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CLINICAL_TRIALS trial_result · 2026-01-21Clinical Trial Update: Effect of Oral Cimetidine in the Protoporphyrias [Phase 2]
A Phase 2 trial evaluating oral cimetidine for erythropoietic protoporphyria and X-linked protoporphyria has completed, reporting results on…
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CLINICAL_TRIALS trial_result · 2026-01-08Clinical Trial Update: Study of Bitopertin to Evaluate the Safety, Tolerability, Efficacy, and PPIX Concentrations in Participants With EPP [Phase 2]
Phase 2 study of Bitopertin in erythropoietic protoporphyria has completed, with results posted evaluating safety, tolerability, efficacy, a…
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CLINICAL_TRIALS research · 2025-12-18Clinical Trial Update: HELIOS: Open-Label, Long-Term Extension Study to Investigate the Safety, Tolerability, and Efficacy of DISC-1459 (Bitopertin) in Participants With EPP or XLP [Phase 2, Phase 3]
Open-label HELIOS extension study evaluating DISC-1459 (Bitopertin) for safety, tolerability, and efficacy in erythropoietic protoporphyria …
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CLINICAL_TRIALS trial_result · 2025-12-11Clinical Trial Update: INcreased Sun Exposure Without Pain In Research Participants With EPP or XLP [Phase 3]
A Phase 3 clinical trial is assessing whether participants with erythropoietic protoporphyria or X-linked protoporphyria can tolerate more s…
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CLINICAL_TRIALS research · 2025-12-11Clinical Trial Update: Extension Study to Evaluate Safety and Tolerability of Oral Dersimelagon (MT-7117) in Subjects With Erythropoietic Protoporphyria (EPP) or X-Linked Protoporphyria (XLP) [Phase 3]
An extension study in Phase 3 to evaluate the safety and tolerability of oral dersimelagon (MT-7117) in subjects with erythropoietic protopo…
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CLINICAL_TRIALS research · 2025-05-14Clinical Trial Update: GATEWAY: A Phase 2a Study of PORT-77 in Adults With Erythropoietic Protoporphyria [Phase 2]
A Phase 2a clinical trial update for PORT-77 in adults with erythropoietic protoporphyria, currently enrolling by invitation.
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CLINICAL_TRIALS trial_result · 2025-03-21Clinical Trial Update: Study to Evaluate Efficacy, Safety, and Tolerability of MT-7117 in Subjects With Erythropoietic Protoporphyria or X-Linked Protoporphyria [Phase 3]
A Phase 3 trial evaluating MT-7117 in erythropoietic protoporphyria and X-linked protoporphyria has completed, with results posted.
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CLINICAL_TRIALS trial_result · 2023-01-20Clinical Trial Update: Study to Evaluate Efficacy, Safety, and Tolerability of MT-7117 in Subjects With Erythropoietic Protoporphyria [Phase 2]
Phase 2 trial of MT-7117 in Erythropoietic Protoporphyria has completed and results have been posted. The study, sponsored by Tanabe Pharma …
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CLINICAL_TRIALS trial_result · 2021-10-12Clinical Trial Update: Phase III Confirmatory Study in Erythropoietic Protoporphyria (EPP) [Phase 3]
A Phase III confirmatory study in erythropoietic protoporphyria has completed with results posted in 2021.
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CLINICAL_TRIALS trial_result · 2020-11-02Clinical Trial Update: A Safety Extension Study in Patients With Erythropoietic Protoporphyria (EPP) [Phase 3]
A Phase 3 safety extension study in erythropoietic protoporphyria has completed with results posted in 2020.
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CLINICAL_TRIALS trial_result · 2020-09-11Clinical Trial Update: Oral Iron for Erythropoietic Protoporphyrias [NA]
Clinical trial update for oral iron in patients with erythropoietic protoporphyria; study completed with results posted in 2020. Disease nam…
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CLINICAL_TRIALS research · 2020-04-17Clinical Trial Update: Erythropoietic Protoporphyrias: Studies of the Natural History, Genotype-Phenotype Correlations, and Psychosocial Impact
Clinical trial update focusing on natural history, genotype-phenotype correlations, and psychosocial impact in erythropoietic protoporphyria…