Dystrophinopathy

• CLINICAL_TRIALS research · 2026-02-11
  Clinical Trial Update: Registry for Duchenne and Becker Muscular Dystrophy

  This entry documents a registry study for Duchenne and Becker muscular dystrophy led by Dr. Andreas Ziegler, currently not yet recruiting.

• CLINICAL_TRIALS trial_result · 2020-11-25
  Clinical Trial Update: Study of Ataluren for Previously Treated Participants With Nonsense Mutation Duchenne/Becker Muscular Dystrophy (nmDBMD) in Europe, Israel, Australia, and Canada [Phase 3]

  Phase 3 trial update for ataluren in previously treated nmDBMD participants with nonsense mutation Duchenne/Becker muscular dystrophy; study…