CLINICAL_TRIALS
trial_result
· 2020-11-25
Clinical Trial Update: Study of Ataluren for Previously Treated Participants With Nonsense Mutation Duchenne/Becker Muscular Dystrophy (nmDBMD) in Europe, Israel, Australia, and Canada [Phase 3]
Summary
Phase 3 trial update for ataluren in previously treated nmDBMD participants with nonsense mutation Duchenne/Becker muscular dystrophy; study completed with resu…
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Snippet
Sponsor: PTC Therapeutics | Conditions: Duchenne Muscular Dystrophy, Becker Muscular Dystrophy | Phase 3 | Status: COMPLETED | Results posted: 2020-11-25