Dyskeratosis Congenita
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2026-04-14Clinical Trial Update: Cancer in Inherited Bone Marrow Failure Syndromes
This clinical trial is currently recruiting to study cancer in inherited bone marrow failure syndromes, including Diamond Blackfan Anemia, D…
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CLINICAL_TRIALS trial_result · 2026-03-27Clinical Trial Update: Radiation- and Alkylator-free Bone Marrow Transplantation Regimen for Patients With Dyskeratosis Congenita [Phase 2]
Phase 2 clinical trial update describing a radiation- and alkylator-free bone marrow transplantation regimen for patients with Dyskeratosis …
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CLINICAL_TRIALS research · 2026-03-18Clinical Trial Update: Nucleoside Therapy in Patients With Telomere Biology Disorders [Phase 1]
Phase 1 clinical trial evaluating nucleoside therapy in patients with telomere biology disorders is currently recruiting.
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CLINICAL_TRIALS research · 2026-02-18Clinical Trial Update: Expanded Access to CD34+ Selection Utilizing Miltenyi CliniMACS Prodigy® for Patients Receiving Peripheral Blood Stem Cell Transplantations and Stem Cell Boosts
This clinical trial update describes expanded access to CD34+ selection using the Miltenyi CliniMACS Prodigy for patients receiving peripher…
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CLINICAL_TRIALS research · 2026-01-30Clinical Trial Update: Alpha/Beta TCD HCT in Patients With Inherited BMF Disorders [Phase 2]
Phase 2 clinical trial update investigating alpha/beta T cell receptor alpha/beta-depleted hematopoietic cell transplantation in inherited b…
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CLINICAL_TRIALS research · 2025-11-28Clinical Trial Update: Regenerative Medicine to Restore Hematopoiesis and Immune Function in Immunodeficiencies and Inherited Bone Marrow Failures [Phase 2]
Phase 2 clinical trial update on regenerative medicine to restore hematopoiesis and immune function in immunodeficiencies and inherited bone…
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CLINICAL_TRIALS research · 2025-11-04Clinical Trial Update: Investigation of the Genetics of Hematologic Diseases
A St. Jude-sponsored clinical trial update indicates a study on the genetics of hematologic diseases is currently recruiting, covering sever…
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CLINICAL_TRIALS trial_result · 2025-08-05Clinical Trial Update: The TELO-SCOPE Study: Attenuating Telomere Attrition With Danazol. Is There Scope to Dramatically Improve Health Outcomes for Adults and Children With Pulmonary Fibrosis [Phase 2]
The Phase 2 TELO-SCOPE study evaluating danazol to attenuate telomere attrition in pulmonary fibrosis has been terminated.
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CLINICAL_TRIALS trial_result · 2025-05-08Clinical Trial Update: Hematopoietic Stem Cell Transplant for Dyskeratosis Congenita or Severe Aplastic Anemia [NA]
A completed clinical trial investigating hematopoietic stem cell transplantation for Dyskeratosis Congenita or Severe Aplastic Anemia has po…
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CLINICAL_TRIALS trial_result · 2024-12-11Clinical Trial Update: Needs Assessment for Individuals and Families Affected by Dyskeratosis Congenita (DC) and Related Telomere Biology Disorders (TBD)
Completion of a National Cancer Institute–sponsored needs assessment study examining the needs of individuals and families affected by Dyske…
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CLINICAL_TRIALS trial_result · 2019-02-19Clinical Trial Update: Safety and Efficacy Trial of Danazol in Patients With Fanconi Anemia or Dyskeratosis Congenita [Phase 1, Phase 2]
The Phase 1/2 safety and efficacy trial of danazol in patients with Fanconi anemia or Dyskeratosis Congenita was terminated, and results hav…
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CLINICAL_TRIALS trial_result · 2017-05-31Clinical Trial Update: Stem Cell Transplant (SCT) for Dyskeratosis Congenita or SAA [Phase 2, Phase 3]
Completed Phase 2 and Phase 3 clinical trial evaluating stem cell transplant for Dyskeratosis Congenita and Aplastic Anemia; results posted …
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CLINICAL_TRIALS trial_result · 2015-01-16Clinical Trial Update: Assessing Immune Function in Young Patients With Cytopenia That Did Not Respond to Treatment
A completed clinical trial from University Hospital Freiburg evaluating immune function in young cytopenia patients unresponsive to treatmen…