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CLINICAL_TRIALS trial_result · 2026-03-27

Clinical Trial Update: Radiation- and Alkylator-free Bone Marrow Transplantation Regimen for Patients With Dyskeratosis Congenita [Phase 2]

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Summary

Phase 2 clinical trial update describing a radiation- and alkylator-free bone marrow transplantation regimen for patients with Dyskeratosis Congenita and relate…

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Diseases / indications

Snippet

Sponsor: Boston Children's Hospital | Conditions: Dyskeratosis Congenita, Hoyeraal Hreidarsson Syndrome | Phase 2 | Status: ACTIVE_NOT_RECRUITING