CLINICAL_TRIALS
trial_result
· 2026-03-27
Clinical Trial Update: Radiation- and Alkylator-free Bone Marrow Transplantation Regimen for Patients With Dyskeratosis Congenita [Phase 2]
Summary
Phase 2 clinical trial update describing a radiation- and alkylator-free bone marrow transplantation regimen for patients with Dyskeratosis Congenita and relate…
Upgrade for the full analysis, importance score, and drug timeline.
Diseases / indications
Snippet
Sponsor: Boston Children's Hospital | Conditions: Dyskeratosis Congenita, Hoyeraal Hreidarsson Syndrome | Phase 2 | Status: ACTIVE_NOT_RECRUITING