Duchenne Muscular Dystrophy
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CLINICAL_TRIALS research · 2026-02-27Clinical Trial Update: Duchenne Muscular Dystrophy and the Viscoelastic Properties of Upper Limb Muscles
An ongoing clinical trial at Sanko University is studying Duchenne muscular dystrophy and the viscoelastic properties of upper limb muscles,…
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CLINICAL_TRIALS research · 2026-02-25Clinical Trial Update: Evaluation of the Role of miR-1 in the Pathogenesis and as a Biomarker in Muscular Dystrophies and Congenital Myopathies [NA]
A clinical trial is recruiting to evaluate the role of microRNA-1 (miR-1) in disease pathogenesis and as a biomarker for muscular dystrophie…
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CLINICAL_TRIALS research · 2026-02-23Clinical Trial Update: Investigation of the Relationship Between Executive Functions and Occupational Performance of Children With Duchenne Muscular Dystrophy
This clinical trial from Lokman Hekim University is investigating the relationship between executive functions and occupational performance …
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CLINICAL_TRIALS research · 2026-02-20Clinical Trial Update: A Remote Study Using Technology to Assess Outcomes in DMD
The trial update describes a remote, technology-enabled study to assess outcomes in Duchenne Muscular Dystrophy. Recruitment has not yet beg…
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CLINICAL_TRIALS research · 2026-02-12Clinical Trial Update: Natural History of Duchenne Muscular Dystrophy
This entry describes an ongoing clinical trial studying the natural history of Duchenne Muscular Dystrophy, sponsored by Genethon, which is …
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CLINICAL_TRIALS research · 2026-02-11Clinical Trial Update: Registry for Duchenne and Becker Muscular Dystrophy
This entry documents a registry study for Duchenne and Becker muscular dystrophy led by Dr. Andreas Ziegler, currently not yet recruiting.
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CLINICAL_TRIALS research · 2026-02-10Clinical Trial Update: A Gene Delivery Study to Evaluate the Safety and Expression of Delandistrogene Moxeparvovec in Participants Under the Age of Four With Duchenne Muscular Dystrophy (DMD) [Phase 2]
This clinical trial update shows Roche's delandistrogene moxeparvovec being studied in children under four with Duchenne Muscular Dystrophy …
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CLINICAL_TRIALS research · 2026-01-30Clinical Trial Update: Multiparametric Ultrafast Ultrasound Biomarkers for Duchenne and Becker Muscular Dystrophies
A clinical trial update describes multiparametric ultrafast ultrasound biomarkers being studied for Duchenne muscular dystrophy and Becker m…
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CLINICAL_TRIALS research · 2026-01-29Clinical Trial Update: Factors Influencing Physical Activity Levels in Children With Duchenne Muscular Dystrophy: An ICF-CY-Based Study
This update reports a clinical trial evaluating factors that influence physical activity levels in children with Duchenne muscular dystrophy…
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CLINICAL_TRIALS research · 2026-01-27Clinical Trial Update: Gamified Occupational Therapy for Adolescents With Duchenne Muscular Dystrophy [NA]
A clinical trial update shows that a gamified occupational therapy program is recruiting adolescents with Duchenne Muscular Dystrophy.
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CLINICAL_TRIALS research · 2026-01-27Clinical Trial Update: The Effect of Dual-tasking Program on Cognitive and Physical Functions and Independence in Activities of Daily Living in Children With Duchenne Muscular Dystrophy: A Single-blind Randomized Controlled Trial [NA]
This clinical trial is enrolling by invitation to study whether a dual-tasking program improves cognitive and physical function and independ…
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CLINICAL_TRIALS research · 2026-01-27Clinical Trial Update: DMD and Gamified Physiotherapy [NA]
The document reports an update on a Duchenne Muscular Dystrophy trial investigating gamified physiotherapy. The study is currently not yet r…
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CLINICAL_TRIALS research · 2026-01-22Clinical Trial Update: Self-Efficacy Enhancement Using a Multicomponent Support Group for Caregivers of Children With DMD/SMA [NA]
This clinical trial update describes a study to enhance self-efficacy in caregivers of children with Duchenne Muscular Dystrophy and Spinal …
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CLINICAL_TRIALS research · 2026-01-21Clinical Trial Update: Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study [Phase 2, Phase 3]
This clinical trial update reports a phase 2/3 long-term safety and tolerability study of givinostat for Duchenne muscular dystrophy, curren…
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CLINICAL_TRIALS research · 2026-01-20Clinical Trial Update: Expanded Access Protocol for Boys With Duchenne Muscular Dystrophy
This update covers an Expanded Access Protocol for boys with Duchenne Muscular Dystrophy sponsored by Santhera Pharmaceuticals.
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CLINICAL_TRIALS research · 2026-01-16Clinical Trial Update: A Study to Evaluate the Safety and Tolerability of RAG-18 in Pediatric Patients With Duchenne Muscular Dystrophy [EARLY_Phase 1]
A pediatric Phase 1 study evaluating safety and tolerability of the investigational drug RAG-18 in Duchenne muscular dystrophy is active but…
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CLINICAL_TRIALS research · 2026-01-15Clinical Trial Update: Swiss Registry for Neuromuscular Disorders
The University of Bern is coordinating a Swiss registry for neuromuscular disorders with ongoing recruitment, covering multiple conditions i…
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CLINICAL_TRIALS research · 2025-12-24Clinical Trial Update: Sodium/Glucose Cotransporter-2 Inhibitors (SGLT2i) Therapy in Duchenne Cardiomyopathy [Phase 1]
Phase 1 clinical trial assessing SGLT2 inhibitors as therapy for Duchenne cardiomyopathy in Duchenne muscular dystrophy; recruitment not yet…
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CLINICAL_TRIALS research · 2025-12-17Clinical Trial Update: A Study of Deramiocel (CAP-1002) in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy [Phase 3]
This clinical trial update reports that Capricor's Phase 3 study of Deramiocel (CAP-1002) in Duchenne muscular dystrophy is currently active…
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CLINICAL_TRIALS research · 2025-12-17Clinical Trial Update: AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD) [Phase 2, Phase 3]
A status update that RGX-202 gene therapy for Duchenne Muscular Dystrophy is in Phase 2/3 and currently recruiting.
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CLINICAL_TRIALS research · 2025-12-16Clinical Trial Update: Active NBS Study: Decentralised Monitoring Motor Development in Children With Duchenne Muscular Dystrophy or Spinal Muscular Atrophy Identified by Newborn Screening [NA]
An ongoing newborn-screening study evaluating decentralized monitoring of motor development in children with spinal muscular atrophy or Duch…
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CLINICAL_TRIALS research · 2025-12-15Clinical Trial Update: Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53) [Phase 1, Phase 2]
An open-label Phase 1/2 study (FORWARD-53) of WVE-N531 in Duchenne Muscular Dystrophy is currently recruiting.
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CLINICAL_TRIALS research · 2025-12-15Clinical Trial Update: The Baby Duchenne Study: Characterizing Developmental and Clinical Outcomes in the First Three Years in Children With Duchenne Muscular Dystrophy
The Baby Duchenne Study is a pediatric clinical trial evaluating developmental and clinical outcomes during the first three years of life in…
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CLINICAL_TRIALS research · 2025-12-04Clinical Trial Update: A Clinical Study to Evaluate the Safety, Tolerability, and Efficacy of BBM-D101 in the Treatment of Duchenne Muscular Dystrophy. [Phase 1, Phase 2]
A clinical trial update describes a Phase 1/2 study to evaluate safety, tolerability, and efficacy of BBM-D101 in Duchenne muscular dystroph…
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CLINICAL_TRIALS research · 2025-12-02Clinical Trial Update: An Observational Study Comparing Delandistrogene Moxeparvovec With Standard of Care in Participants With Duchenne Muscular Dystrophy
An observational study comparing Delandistrogene Moxeparvovec with standard of care in Duchenne muscular dystrophy is currently enrolling by…