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CLINICAL_TRIALS research · 2025-12-16

Clinical Trial Update: Active NBS Study: Decentralised Monitoring Motor Development in Children With Duchenne Muscular Dystrophy or Spinal Muscular Atrophy Identified by Newborn Screening [NA]

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Summary

An ongoing newborn-screening study evaluating decentralized monitoring of motor development in children with spinal muscular atrophy or Duchenne muscular dystro…

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Diseases / indications

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Sponsor: Centre Hospitalier Universitaire de Liege | Conditions: Spinal Muscular Atrophy (SMA), Duchenne Muscular Dystrophy (DMD) | NA | Status: RECRUITING