Dravet Syndrome
📧 Sign up to get email alerts when something new happens for Dravet Syndrome.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS research · 2026-04-21Clinical Trial Update: ASCEND: Safety and Tolerability of ION337 for the Treatment of Dravet Syndrome [Phase 1, Phase 2]
Ongoing Phase 1/2 ASCEND trial evaluating the safety and tolerability of Ionis' antisense therapy ION337 for Dravet syndrome; trial status i…
-
CLINICAL_TRIALS research · 2026-04-16Clinical Trial Update: A Clinical Study to Evaluate the Safety and Efficacy of ETX101 in Infants and Children With SCN1A-Positive Dravet Syndrome [Phase 1, Phase 2]
A Phase 1/2 clinical study is evaluating the safety and efficacy of ETX101 in infants and children with SCN1A-positive Dravet syndrome, and …
-
CLINICAL_TRIALS research · 2026-04-15Clinical Trial Update: A Phase 3, Placebo-Controlled Study to Investigate LP352 in Children and Adults With Dravet Syndrome (DS) [Phase 3]
A Phase 3, placebo-controlled study evaluating LP352 in children and adults with Dravet syndrome is currently recruiting.
-
CLINICAL_TRIALS research · 2026-04-13Clinical Trial Update: A Double-blind Study Evaluating the Efficacy, Safety, and Tolerability of Zorevunersen in Patients With Dravet Syndrome [Phase 3]
Phase 3 double-blind trial evaluating Zorevunersen for Dravet syndrome is currently recruiting to assess efficacy, safety, and tolerability.
-
CLINICAL_TRIALS research · 2026-04-03Clinical Trial Update: A Study to Evaluate Safety, Tolerability, and Pharmacokinetics of Fenfluramine (Hydrochloride) in Infants 1 Year to Less Than 2 Years of Age With Dravet Syndrome [Phase 3]
This Phase 3 clinical study is evaluating the safety, tolerability, and pharmacokinetics of fenfluramine hydrochloride in infants aged 1 yea…
- Want full summaries, importance scores, and drug timelines? Upgrade to Plus or Pro.
-
CLINICAL_TRIALS research · 2026-04-03Clinical Trial Update: The FINTEPLA as an Anti-SUDEP Therapy in Dravet Syndrome Project [Phase 4]
Phase 4 clinical trial update for FINTEPLA (fenfluramine) as an anti-SUDEP therapy in Dravet syndrome. The study is not yet recruiting.
-
CLINICAL_TRIALS research · 2026-03-17Clinical Trial Update: A Study to Investigate the Transition of Children From 'Artisanal" Cannabidiol (CBD) to Epidiolex [Phase 4]
A Phase 4 study is evaluating how children with Dravet syndrome or Lennox-Gastaut syndrome transition from artisanal cannabidiol to Epidiole…
-
CLINICAL_TRIALS research · 2026-02-27Clinical Trial Update: A PET-MRI Study of Serotoninergic Brainstem Pathway in Patients With Dravet Syndrome [NA]
This registry entry outlines a PET-MRI study of serotoninergic brainstem pathways in patients with Dravet syndrome and epilepsy. The trial s…
-
CLINICAL_TRIALS research · 2026-02-24Clinical Trial Update: Multicentre Real-life Follow-up Study of Rare Epileptic Syndromes in Children and Adolescents
This multicentre real-life follow-up study aims to characterize rare epileptic syndromes in children and adolescents, including West syndrom…
-
CLINICAL_TRIALS research · 2026-02-17Clinical Trial Update: Epidyolex® in Lennox Gastaut, Dravet Syndrome and Tuberous Sclerosis Complex: an Observational Study in ITALY
An observational study of Epidyolex (cannabidiol) in Lennox-Gastaut syndrome, Dravet syndrome, and tuberous sclerosis complex is currently r…
-
CLINICAL_TRIALS research · 2026-02-04Clinical Trial Update: An Open-Label Extension Study of STK-001 for Patients With Dravet Syndrome [Phase 2]
Open-label extension update for STK-001 in Dravet syndrome within a Phase 2 trial; the study is active but not recruiting.
-
CLINICAL_TRIALS research · 2026-02-03Clinical Trial Update: Longitudinal Study of Phenotypic and Developmental Severity in Patients With Dravet Syndrome With SCN1A Gene Mutation
A longitudinal observational study in Dravet syndrome patients with SCN1A mutation is currently recruiting to characterize phenotypic and de…
-
CLINICAL_TRIALS research · 2025-12-12Clinical Trial Update: A Clinical Study to Evaluate the Safety and Efficacy of ETX101, an AAV9-Delivered Gene Therapy in Children With SCN1A-positive Dravet Syndrome [Phase 1, Phase 2]
A clinical study evaluating the safety and efficacy of ETX101, an AAV9-delivered gene therapy, in children with SCN1A-positive Dravet syndro…
-
CLINICAL_TRIALS research · 2025-11-14Clinical Trial Update: A Clinical Study to Evaluate the Safety and Efficacy of ETX101, an AAV9-Delivered Gene Therapy in Children With SCN1A-positive Dravet Syndrome (Australia Only) [Phase 1, Phase 2]
Clinical trial update for ETX101, an AAV9-delivered gene therapy for SCN1A-positive Dravet syndrome, currently in Phase 1/Phase 2 in Austral…
-
CLINICAL_TRIALS research · 2025-11-06Clinical Trial Update: Clinical Utility of Reduced EEG Home Monitoring in Fenfluramine Titration for Dravet and LGS [NA]
This clinical trial update describes a study on reduced EEG home monitoring during fenfluramine titration for Dravet syndrome and Lennox-Gas…
-
CLINICAL_TRIALS research · 2025-08-28Clinical Trial Update: A Study of EPX-100 (Clemizole Hydrochloride) in Participants With Dravet Syndrome [Phase 3]
EPX-100 (clemizole hydrochloride) is advancing to Phase 3 for Dravet syndrome and is currently recruiting participants.
-
CLINICAL_TRIALS research · 2025-08-12Clinical Trial Update: BMB-101 in Absence Epilepsy and DEE [Phase 2]
Phase 2 clinical trial update for BMB-101 in absence epilepsy and developmental and epileptic encephalopathies, including Jeavons syndrome, …
-
CLINICAL_TRIALS research · 2025-05-18Clinical Trial Update: An Open-Label Study to Investigate the Safety of Single and Multiple Ascending Doses in Children and Adolescents With Dravet Syndrome [Phase 1, Phase 2]
This entry reports the completion of an open-label Phase 1/2 study evaluating safety of single and multiple ascending doses of STK-001 in ch…
-
CLINICAL_TRIALS research · 2025-04-17Clinical Trial Update: A Study to Gather Information About Overall Occurrence and New Cases of Dravet and Lennox-Gastaut Syndromes in Children, Teenagers and Adults in Spain
This completed Spanish registry study collected information on how often Dravet syndrome and Lennox-Gastaut syndrome occur and new cases acr…
-
CLINICAL_TRIALS research · 2025-01-22Clinical Trial Update: Intermediate-Size Expanded Access Protocol (EAP) for LP352
Update on Longboard Pharmaceuticals' expanded access protocol for LP352, indicating availability for patients with Dravet syndrome, Lennox-G…
-
CLINICAL_TRIALS research · 2024-12-18Clinical Trial Update: CBD Delivery with the A-Synaptic GT4 Transdermal Delivery System in with Dravet Syndrome And/or Lennox-Gastaut Syndrome [Phase 1, Phase 2]
This clinical trial update describes a Phase 1/Phase 2 study evaluating cannabidiol delivered via the A-Synaptic GT4 transdermal system for …
-
CLINICAL_TRIALS research · 2024-12-10Clinical Trial Update: Assessment of Safety of the Use of Fenfluramine in Children With Dravet Syndrome Under 24 Months of Age [Phase 4]
Phase 4 clinical trial assessing the safety of fenfluramine in children with Dravet syndrome under 24 months; currently recruiting.
-
CLINICAL_TRIALS research · 2024-07-16Clinical Trial Update: SCN1A Horizons A Natural History Study of SCN1A-related Epilepsies in the United Kingdom
ClinicalTrials.gov reports a UK natural history study of SCN1A-related epilepsies that is currently recruiting to better characterize diseas…