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CLINICAL_TRIALS research · 2025-11-14

Clinical Trial Update: A Clinical Study to Evaluate the Safety and Efficacy of ETX101, an AAV9-Delivered Gene Therapy in Children With SCN1A-positive Dravet Syndrome (Australia Only) [Phase 1, Phase 2]

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Summary

Clinical trial update for ETX101, an AAV9-delivered gene therapy for SCN1A-positive Dravet syndrome, currently in Phase 1/Phase 2 in Australia and not recruitin…

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Diseases / indications

Drugs mentioned

  • ETX101

Snippet

Sponsor: Encoded Therapeutics | Conditions: Dravet Syndrome | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING