CLINICAL_TRIALS
research
· 2025-11-14
Clinical Trial Update: A Clinical Study to Evaluate the Safety and Efficacy of ETX101, an AAV9-Delivered Gene Therapy in Children With SCN1A-positive Dravet Syndrome (Australia Only) [Phase 1, Phase 2]
Summary
Clinical trial update for ETX101, an AAV9-delivered gene therapy for SCN1A-positive Dravet syndrome, currently in Phase 1/Phase 2 in Australia and not recruitin…
Upgrade for the full analysis, importance score, and drug timeline.
Diseases / indications
Drugs mentioned
Snippet
Sponsor: Encoded Therapeutics | Conditions: Dravet Syndrome | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING