D-bifunctional Protein Deficiency
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CLINICAL_TRIALS research · 2025-12-10Clinical Trial Update: Longitudinal Natural History Study of Patients With Peroxisome Biogenesis Disorders (PBD)
An ongoing longitudinal natural history study for patients with peroxisome biogenesis disorders (including Zellweger spectrum disorders) is …
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CLINICAL_TRIALS trial_result · 2015-03-25Clinical Trial Update: Study of Bile Acids in Patients With Peroxisomal Disorders [NA]
A clinical trial evaluating bile acids for peroxisomal disorders has been terminated, involving diseases such as Infantile Refsum's Disease …