Clinical Trial Update: Longitudinal Natural History Study of Patients With Peroxisome Biogenesis Disorders (PBD)

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Summary

An ongoing longitudinal natural history study for patients with peroxisome biogenesis disorders (including Zellweger spectrum disorders) is currently recruiting…

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Diseases / indications

• Alpha-methylacyl-coa Racemase Deficiency
• D-bifunctional Protein Deficiency
• Peroxisomal Acyl-coa Oxidase Deficiency
• Peroxisome Biogenesis Disorder
• Refsum Disease
• Rhizomelic Chondrodysplasia Punctata
• Zellweger Spectrum Disorder

Snippet

Sponsor: McGill University Health Centre/Research Institute of the McGill University Health Centre | Conditions: Peroxisome Biogenesis Disorder, Zellweger Spectrum Disorder | Status: RECRUITING