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CLINICAL_TRIALS ClinicalTrials.gov record update

Longitudinal Natural History Study of Patients With Peroxisome Biogenesis Disorders (PBD)

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Record identity and dates

Source
ClinicalTrials.gov
Source record ID
NCT01668186
Title field or adapter rule
protocolSection.identificationModule.officialTitle
Ingested At
2026-04-25T22:28:51.046045+00:00
Published At
2025-12-10T00:00:00+00:00
Record Updated At
2025-12-10
Timestamp Basis
source retrieval time was not retained by the feed adapter
Date limitation
source retrieval time was not retained by the feed adapter

Fields recorded by this source

protocolSection.conditionsModule.conditions
["Peroxisome Biogenesis Disorder", "Zellweger Spectrum Disorder", "RCDP - Rhizomelic Chondrodysplasia Punctata", "D-Bifunctional Protein Deficiency", "Alpha-Methylacyl-CoA Racemase Deficiency", "Peroxisomal Acyl-CoA Oxidase Deficiency", "Peroxisomal Acyl-CoA Oxidase 2 Deficiency", "ATP Binding Cassette Subfamily D Member 3 Gene Mutation", "ACBD5 (AcylCoA Binding Domain 5) Deficiency", "Adult Refsum Disease", "Sterol Carrier Protein 2 Deficiency"]
protocolSection.statusModule.lastUpdatePostDateStruct.date
"2025-12-10"
protocolSection.identificationModule.nctId
"NCT01668186"
protocolSection.identificationModule.officialTitle
"Longitudinal Natural History Study of Patients With Peroxisome Biogenesis Disorders (PBD)"
protocolSection.statusModule.overallStatus
"RECRUITING"
protocolSection.designModule.phases
[]
protocolSection.statusModule.resultsFirstPostDateStruct.date
""

Study condition terms

  • Peroxisome Biogenesis Disorder (protocolSection.conditionsModule.conditions)
  • Zellweger Spectrum Disorder (protocolSection.conditionsModule.conditions)
  • RCDP - Rhizomelic Chondrodysplasia Punctata (protocolSection.conditionsModule.conditions)
  • D-Bifunctional Protein Deficiency (protocolSection.conditionsModule.conditions)
  • Alpha-Methylacyl-CoA Racemase Deficiency (protocolSection.conditionsModule.conditions)
  • Peroxisomal Acyl-CoA Oxidase Deficiency (protocolSection.conditionsModule.conditions)
  • Peroxisomal Acyl-CoA Oxidase 2 Deficiency (protocolSection.conditionsModule.conditions)
  • ATP Binding Cassette Subfamily D Member 3 Gene Mutation (protocolSection.conditionsModule.conditions)
  • ACBD5 (AcylCoA Binding Domain 5) Deficiency (protocolSection.conditionsModule.conditions)
  • Adult Refsum Disease (protocolSection.conditionsModule.conditions)
  • Sterol Carrier Protein 2 Deficiency (protocolSection.conditionsModule.conditions)

Intervention details are not present in the imported fields for this record. No drug-condition relationship is inferred from co-listing.

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