Cystic Fibrosis
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CLINICAL_TRIALS research · 2026-01-05Clinical Trial Update: Lung Transplant READY CF 2: A Multi-site RCT [NA]
An update on the Lung Transplant READY CF 2 multi-site randomized trial in cystic fibrosis; the study is currently active but not recruiting…
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CLINICAL_TRIALS research · 2025-12-31Clinical Trial Update: Study to Enable New Diagnostics for Pulmonary Microbes in People With CF
A clinical trial update describes a study aimed at enabling new diagnostics for pulmonary microbes in people with cystic fibrosis. The trial…
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CLINICAL_TRIALS research · 2025-12-31Clinical Trial Update: Natural History Study of Exocrine Pancreatic Function in Infants With Cystic Fibrosis (CF)
This document reports a completed update on the natural history study of exocrine pancreatic function in infants with cystic fibrosis. The s…
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CLINICAL_TRIALS research · 2025-12-29Clinical Trial Update: A Double-Blind, Active-Controlled, Multiple-Ascending Dose Study of Aerosolized RSP-1502 in Subjects With CF and Chronic PA Lung Infection [Phase 1, Phase 2]
A double-blind, active-controlled Phase 1/2 study of aerosolized RSP-1502 in cystic fibrosis patients with chronic Pseudomonas aeruginosa lu…
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CLINICAL_TRIALS research · 2025-12-29Clinical Trial Update: Dose Escalation Study Evaluating the Safety and Pharmacokinetics of VX-581 in Healthy Participants [Phase 1]
A Phase 1 dose-escalation study to evaluate the safety and pharmacokinetics of VX-581 in healthy participants, sponsored by Vertex Pharmaceu…
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CLINICAL_TRIALS trial_result · 2025-12-26Clinical Trial Update: Feasibility of a New Model for Exercise Prescription in Cystic Fibrosis [NA]
A completed clinical trial evaluated the feasibility of a new model for prescribing exercise in people with cystic fibrosis.
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CLINICAL_TRIALS research · 2025-12-26Clinical Trial Update: The School-Age Children With Cystic Fibrosis and Their Parents on Health Literacy [NA]
This clinical trial update indicates ongoing recruitment for a study evaluating health literacy among school-age children with cystic fibros…
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CLINICAL_TRIALS trial_result · 2025-12-22Clinical Trial Update: A Phase 1b/2 Trial of the Safety and Microbiological Activity of Bacteriophage Therapy in Cystic Fibrosis Subjects Colonized With Pseudomonas Aeruginosa [Phase 1, Phase 2]
Results from a completed Phase 1b/2 trial evaluate the safety and microbiological activity of a bacteriophage therapy in cystic fibrosis pat…
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CLINICAL_TRIALS research · 2025-12-19Clinical Trial Update: Nutrition Supplement for Cystic Fibrosis [NA]
Clinical trial entry for a nutrition supplement being studied in cystic fibrosis patients; the study status is not yet recruiting.
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CLINICAL_TRIALS research · 2025-12-19Clinical Trial Update: High Resolution Micro OCT Imaging
A clinical trial update indicates the High Resolution Micro OCT Imaging study led by the University of Alabama at Birmingham is currently ac…
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CLINICAL_TRIALS research · 2025-12-19Clinical Trial Update: GERD in Children With Cystic Fibrosis [NA]
This clinical trial update notes an ongoing study evaluating gastroesophageal reflux disease in children with cystic fibrosis, and it is cur…
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CLINICAL_TRIALS trial_result · 2025-12-17Clinical Trial Update: Study of ARO-ENaC in Healthy Volunteers and in Patients With Cystic Fibrosis [Phase 1, Phase 2]
Clinical trial update shows ARO-ENaC was studied in healthy volunteers and patients with cystic fibrosis (Phase 1/2) and the study is termin…
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CLINICAL_TRIALS research · 2025-12-17Clinical Trial Update: Early Study on Tamoxifen Safety/Tolerability in Cystic Fibrosis Patients Unable to Use CFTR Modulators. [Phase 2]
Phase 2 early study evaluating the safety and tolerability of tamoxifen in cystic fibrosis patients unable to use CFTR modulators; status in…
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CLINICAL_TRIALS research · 2025-12-17Clinical Trial Update: Novel Sensors and Artificial Intelligence for Detection of Acute Pulmonary Exacerbations in Cystic Fibrosis and Bronchiectasis
A clinical trial entry describing a study using novel sensors and artificial intelligence to detect acute pulmonary exacerbations in cystic …
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CLINICAL_TRIALS research · 2025-12-16Clinical Trial Update: Sinonasal Therapies and Histologic Correlations of Patients With Cystic Fibrosis in the Era of Highly Effective Modulator Therapy [Phase 3]
Phase 3 clinical trial update examining sinonasal therapies and histologic correlations in patients with cystic fibrosis and chronic rhinosi…
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CLINICAL_TRIALS research · 2025-12-16Clinical Trial Update: Impact of Highly Effective Modulator Therapy on the Cystic Fibrosis Microbiome
A clinical trial update indicates recruitment is ongoing to study the impact of Highly Effective Modulator Therapy on the cystic fibrosis mi…
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CLINICAL_TRIALS research · 2025-12-12Clinical Trial Update: Safety of Combined Intravenous Antibiotic and Bacteriophage Therapy in Adults With Cystic Fibrosis and Antibiotic-Resistant Lung Infections [Phase 1]
Phase 1 trial update describing safety considerations for combining intravenous antibiotics with bacteriophage therapy in adults with cystic…
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CLINICAL_TRIALS trial_result · 2025-12-12Clinical Trial Update: PACE CF, a 3-session Mind-body Pain Management Program for Adults With Cystic Fibrosis [NA]
The PACE CF trial evaluating a three-session mind-body pain management program for adults with cystic fibrosis has completed.
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CLINICAL_TRIALS trial_result · 2025-12-12Clinical Trial Update: Evaluation of (R)-Roscovitine Safety and Effects in Subjects With Cystic Fibrosis, Homozygous for the F508del-CFTR Mutation [Phase 2]
Phase 2 trial evaluating the safety and effects of (R)-roscovitine in subjects with cystic fibrosis who are homozygous for the F508del-CFTR …
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EMA approval · 2025-12-11EMA Authorised: Tobi Podhaler (tobramycin) — Viatris Healthcare Limited
EMA authorised Tobi Podhaler (tobramycin) for cystic fibrosis and respiratory tract infections; the marketing authorisation holder is Viatri…
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EMA approval · 2025-12-08EMA Authorised: Symkevi (tezacaftor;ivacaftor) — Vertex Pharmaceuticals (Ireland) Limited
The EMA authorised Symkevi (tezacaftor and ivacaftor) for cystic fibrosis. It has orphan medicine status.
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CLINICAL_TRIALS trial_result · 2025-12-08Clinical Trial Update: Virtual Reality Based Tele-Exercises on Exercise Capacity in Cystic Fibrosis [NA]
A completed clinical trial evaluated virtual reality-based tele-exercises to improve exercise capacity in children with cystic fibrosis.
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CLINICAL_TRIALS research · 2025-12-05Clinical Trial Update: OnTrackCF: Engagement, Feasibility, and Acceptability Study [NA]
Clinical trial update for OnTrackCF, an engagement, feasibility, and acceptability study in cystic fibrosis, currently recruiting.
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CLINICAL_TRIALS trial_result · 2025-12-01Clinical Trial Update: Real-life Follow-up of Cystic Fibrosis Patients Treated With Ivacaftor+Lumacaftor (Orkambi*)
Real-life follow-up study of cystic fibrosis patients treated with the Ivacaftor+Lumacaftor combination (Orkambi) has completed, reporting o…
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CLINICAL_TRIALS research · 2025-12-01Clinical Trial Update: Impact of a Coordinated Dietetic-adapted Physical Activity Program on the Percentage of Lean Body Mass in Adults With Cystic Fibrosis Treated With Elexacaftor-Tezacaftor-Ivacaftor: Multicentre Randomised Controlled Trial [NA]
A multicenter randomized trial is evaluating whether a dietetic-adapted physical activity program can influence lean body mass in adults wit…