Cystic Fibrosis
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2012-07-10Clinical Trial Update: Efficacy and Safety Study of Inhaled Glutathione in Cystic Fibrosis Patients [Phase 2]
Phase 2 trial evaluating inhaled glutathione in cystic fibrosis patients has completed.
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CLINICAL_TRIALS trial_result · 2012-07-10Clinical Trial Update: Early Diagnosis of Diabetes Mellitus in Patients With Cystic Fibrosis [Phase 3]
Phase 3 trial evaluating early diagnosis of diabetes mellitus in cystic fibrosis patients has completed. The entry provides status but does …
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CLINICAL_TRIALS trial_result · 2012-07-03Clinical Trial Update: Study to Evaluate the Safety and Efficacy of Ciprofloxacin (Inhaled) in Patients With Cystic Fibrosis [Phase 2]
Phase 2 study evaluating inhaled ciprofloxacin for safety and efficacy in cystic fibrosis has completed with posted results.
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CLINICAL_TRIALS trial_result · 2012-06-14Clinical Trial Update: Effect of Pioglitazone on Inflammation in Cystic Fibrosis [Phase 1]
A Phase 1 clinical trial assessing pioglitazone for reducing inflammation in cystic fibrosis has completed.
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CLINICAL_TRIALS trial_result · 2012-06-12Clinical Trial Update: Safety, Tolerability and Efficacy of MP-376 Given for 28 Days to Cystic Fibrosis (CF) Patients [Phase 2]
Amgen reports results from a Phase 2 trial of MP-376 in cystic fibrosis patients over 28 days, assessing safety, tolerability, and efficacy.…
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CLINICAL_TRIALS trial_result · 2012-06-08Clinical Trial Update: EZ-2053 in the Prophylaxis of Acute Pulmonary Allograft Rejection [Phase 3]
Phase 3 trial evaluating EZ-2053 for prophylaxis of acute pulmonary allograft rejection; the study is completed and results were posted.
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CLINICAL_TRIALS research · 2012-06-01Clinical Trial Update: The Role of Respiratory Viruses in Exacerbations of Cystic Fibrosis in Adults
The document reports on a completed clinical trial examining the role of respiratory viruses in exacerbations of cystic fibrosis in adults.
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EMA approval · 2012-05-25European Medicines Agency recommends first-in-class medicine for treatment of cystic fibrosis
EMA recommends a first-in-class medicine for treating cystic fibrosis, indicating a pivotal recommendation toward approval for a new mechani…
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FDA approval · 2012-05-17FDA Approved: PERTZYE — Original Application (Digestive Care, Inc.)
PERTZYE (pancrelipase) was approved on an original application for the treatment of exocrine pancreatic insufficiency.
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CLINICAL_TRIALS trial_result · 2012-05-08Clinical Trial Update: Self Drainage in Pediatric Cystic Fibrosis Patients [NA]
The clinical trial evaluating self drainage in pediatric cystic fibrosis patients has completed. The sponsor is Hospices Civils de Lyon.
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CLINICAL_TRIALS trial_result · 2012-04-05Clinical Trial Update: Safety and Tolerability Study of Liquid Alpha1 Proteinase Inhibitor (API) in Subjects With Cystic Fibrosis [Phase 1]
Phase 1 safety and tolerability study of liquid Alpha1 Proteinase Inhibitor in subjects with cystic fibrosis has completed. The trial was sp…
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CLINICAL_TRIALS trial_result · 2012-04-03Clinical Trial Update: Pre-flight Evaluation of Adult Patients With Cystic Fibrosis
This clinical trial update indicates the completion of a study evaluating pre-flight evaluation procedures for adults with cystic fibrosis. …
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CLINICAL_TRIALS trial_result · 2012-03-19Clinical Trial Update: SD Cystic Fibrosis Study [Phase 1]
GlaxoSmithKline's Phase 1 cystic fibrosis trial has completed.
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CLINICAL_TRIALS trial_result · 2012-03-07Clinical Trial Update: The Use of Visual Feedback in Airway Clearance [NA]
This entry notes the completion of a clinical trial at Sheba Medical Center evaluating the use of visual feedback to assist airway clearance…
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FDA approval · 2012-03-01FDA Approved: VIOKACE — Original Application (Aimmune Therapeutics, Inc.)
FDA approved Viokace (pancrelipase) via an original application from Aimmune Therapeutics, establishing a pancrelipase therapy for exocrine …
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CLINICAL_TRIALS trial_result · 2012-02-28Clinical Trial Update: Diabetes Therapy to Improve BMI and Lung Function in CF [Phase 3]
A Phase 3 trial evaluating a diabetes therapy for people with cystic fibrosis has completed, assessing its impact on body mass index and lun…
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CLINICAL_TRIALS trial_result · 2012-02-22Clinical Trial Update: Evaluation of the Safety and Efficacy of Pancrecarb® MS-16 in Cystic Fibrosis [Phase 3]
Phase 3 trial evaluating the safety and efficacy of Pancrecarb MS-16 in cystic fibrosis with pancreatic insufficiency has completed.
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CLINICAL_TRIALS approval · 2012-02-09Clinical Trial Update: VX-770 Expanded Access Program
Ivacaftor (VX-770) has received marketing approval for cystic fibrosis, as noted in Vertex's expanded access program update.
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CLINICAL_TRIALS trial_result · 2012-02-03Clinical Trial Update: Absorptive Clearance in the Cystic Fibrosis Airway [NA]
A completed clinical trial from the University of Pittsburgh on absorptive clearance in the Cystic Fibrosis airway, with results posted in 2…
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FDA approval · 2012-01-31FDA Approved: KALYDECO — Original Application (Vertex Pharmaceuticals Incorporated)
The FDA approved KALYDECO (ivacaftor) through an original application for the treatment of cystic fibrosis in patients with specific CFTR ga…
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CLINICAL_TRIALS trial_result · 2012-01-31Clinical Trial Update: Nasal Potential Studies Utilizing Cystic Fibrosis Transmembrane Regulator (CFTR) Modulators [Phase 2]
This update summarizes Phase 2 nasal potential studies using CFTR modulators for cystic fibrosis; the trial status is completed.
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CLINICAL_TRIALS trial_result · 2012-01-18Clinical Trial Update: Drug-Drug Interaction Study of VX-770 and VX-809 in Healthy Subjects [Phase 1]
Phase 1 drug-drug interaction study evaluating ivacaftor (VX-770) and lumacaftor (VX-809) in healthy subjects to support cystic fibrosis the…
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CLINICAL_TRIALS research · 2012-01-05Clinical Trial Update: Changes in Lung Function Based on Differences in Spirometry Equipment Used in Children With Cystic Fibrosis
This update reports that differences in spirometry equipment used in trials can affect measured lung function in children with cystic fibros…
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CLINICAL_TRIALS research · 2011-11-11Clinical Trial Update: Small Intestinal Function in Patients With Cystic Fibrosis
This entry provides a research update on a clinical trial evaluating small intestinal function in people with cystic fibrosis.
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CLINICAL_TRIALS trial_result · 2011-10-27Clinical Trial Update: Indirect Comparison of Tobramycin Solution for Inhalation Versus Aztreonam Lysine for Inhalation in the Treatment of Cystic Fibrosis
Clinical trial update comparing inhaled tobramycin versus inhaled aztreonam for cystic fibrosis using indirect comparison.