Cystic Fibrosis
📧 Sign up to get email alerts when something new happens for Cystic Fibrosis.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2015-01-07Clinical Trial Update: Dissection of Staphylococcus Aureus Infection From Colonization in Cystic Fibrosis Patients
This completed clinical trial investigated distinguishing Staphylococcus aureus infection from colonization in patients with cystic fibrosis…
-
FDA approval · 2015-01-05FDA Approved: CREON — Supplemental Application (AbbVie Inc.)
The FDA approved a supplemental application for CREON (pancrelipase) from AbbVie, updating its labeling to support its use for exocrine panc…
-
FDA approval · 2015-01-05FDA Approved: KALYDECO — Supplemental Application (Vertex Pharmaceuticals Incorporated)
FDA approved a supplemental application for KALYDECO (ivacaftor) from Vertex Pharmaceuticals Incorporated. This action updates the existing …
-
CLINICAL_TRIALS research · 2014-12-31Clinical Trial Update: Non Ivasive Prenatal Diagnosis (NIPD) of Cystic Fibrosis
Clinical trial update describing noninvasive prenatal diagnosis for cystic fibrosis.
-
FDA approval · 2014-12-29FDA Approved: KALYDECO — Supplemental Application (Vertex Pharmaceuticals Incorporated)
FDA approved a supplemental application for KALYDECO (ivacaftor) submitted by Vertex Pharmaceuticals Incorporated.
- Want full summaries, importance scores, and drug timelines? Upgrade to Plus or Pro.
-
FDA approval · 2014-12-12FDA Approved: PULMOZYME — Supplemental Application (Genentech, Inc.)
FDA approved a supplemental application for Pulmozyme (dornase alfa) filed by Genentech, Inc.
-
FDA approval · 2014-12-11FDA Approved: KALYDECO — Supplemental Application (Vertex Pharmaceuticals Incorporated)
FDA approved a supplemental application for KALYDECO (ivacaftor) submitted by Vertex Pharmaceuticals Incorporated. The approval updates the …
-
CLINICAL_TRIALS research · 2014-12-09Clinical Trial Update: Prospective Observational Study to Evaluate Biomarkers of Aminoglycoside Nephrotoxicity in Patients With Cystic Fibrosis
A prospective observational study to evaluate biomarkers of aminoglycoside nephrotoxicity in cystic fibrosis patients. The study aims to ide…
-
CLINICAL_TRIALS trial_result · 2014-12-05Clinical Trial Update: Sputum Purulence as a Predictor of Cystic Fibrosis Exacerbations: a Prospective Cohort Trial.
A prospective cohort study evaluating whether sputum purulence predicts cystic fibrosis exacerbations. The study has completed recruitment a…
-
CLINICAL_TRIALS trial_result · 2014-12-04Clinical Trial Update: Nasal Inhalation of Pulmozyme in Patients With Cystic Fibrosis and Chronic Rhinosinusitis [Phase 3]
A Phase 3 trial evaluating nasal inhalation of Pulmozyme (dornase alfa) in cystic fibrosis patients with chronic rhinosinusitis has complete…
-
CLINICAL_TRIALS trial_result · 2014-12-04Clinical Trial Update: Nasal Inhalation of Tobramycin in Patients With Cystic Fibrosis and Pseudomonas Aeruginosa Colonization [Phase 2]
Phase 2 clinical trial evaluating nasal inhalation of tobramycin in patients with cystic fibrosis and Pseudomonas aeruginosa colonization; t…
-
CLINICAL_TRIALS trial_result · 2014-12-04Clinical Trial Update: Nasal Inhalation of Dornase Alfa (Pulmozyme) in Patients With Cystic Fibrosis and Chronic Rhinosinusitis [Phase 3]
Phase 3 clinical trial assessing nasal inhalation of dornase alfa (Pulmozyme) in cystic fibrosis patients with chronic rhinosinusitis has co…
-
CLINICAL_TRIALS research · 2014-12-04Clinical Trial Update: Prevalence of Chronic Rhinosinusitis in Cystic Fibrosis
A completed University of Jena clinical trial studied how common chronic rhinosinusitis is in people with cystic fibrosis.
-
CLINICAL_TRIALS trial_result · 2014-12-03Clinical Trial Update: Action of Epigenetic Modifiers in Cystic Fibrosis Treatment [NA]
The document reports on a completed clinical trial assessing the effects of epigenetic modifiers for cystic fibrosis treatment.
-
CLINICAL_TRIALS trial_result · 2014-12-03Clinical Trial Update: Sweat Evaporimeter Measurement [NA]
Clinical trial update reports completion of a University of Colorado, Denver study on cystic fibrosis using sweat evaporimeter measurements.
-
CLINICAL_TRIALS trial_result · 2014-12-02Clinical Trial Update: Cystic Fibrosis Foundation (CFF) Biomarkers of Exacerbation
This clinical trial update reports findings on biomarkers of exacerbation in cystic fibrosis from a completed study led by the University of…
-
CLINICAL_TRIALS trial_result · 2014-12-02Clinical Trial Update: Sino-nasal Inhalation of Sodium Chloride 6,0% in Patients With Cystic Fibrosis and Chronic Rhinosinusitis [NA]
A clinical trial assessing sodium chloride 6.0% sino-nasal inhalation in patients with cystic fibrosis and chronic rhinosinusitis has comple…
-
FDA approval · 2014-12-02FDA Approved: TOBRAMYCIN INHALATION SOLUTION PAK — Original Application (Genericus, Inc.)
FDA approved Genericus, Inc.'s Tobramycin Inhalation Solution Pak, a generic version of tobramycin inhalation solution for patients with cys…
-
CLINICAL_TRIALS trial_result · 2014-11-24Clinical Trial Update: Safety and Pharmacokinetic Study of N6022 in Subjects With Cystic Fibrosis Homozygous for the F508del-CFTR Mutation [Phase 1]
This Clinical Trial Update reports safety and pharmacokinetic results from a Phase 1 study of N6022 in cystic fibrosis patients homozygous f…
-
FDA label_change · 2014-11-21FDA Approved: CREON — Supplemental Application (AbbVie Inc.)
FDA approved a supplemental application for CREON (pancrelipase) from AbbVie, updating the labeling to reflect approved uses for exocrine pa…
-
CLINICAL_TRIALS trial_result · 2014-11-21Clinical Trial Update: Cholecalciferol for Vitamin D in Adult Cystic Fibrosis (CF) Patients [NA]
A completed clinical trial evaluated cholecalciferol (vitamin D3) for treating vitamin D deficiency in adults with cystic fibrosis.
-
CLINICAL_TRIALS trial_result · 2014-11-21Clinical Trial Update: Evaluating the Impact of Chronic Rhinosinusitis on the Health-Related Quality of Life Among Adults With Cystic Fibrosis
This clinical trial update reports completion of a study assessing how chronic rhinosinusitis affects health-related quality of life in adul…
-
FDA approval · 2014-11-19FDA Approved: CREON — Supplemental Application (AbbVie Inc.)
The FDA approved a supplemental application for CREON (pancrelipase) from AbbVie Inc.
-
CLINICAL_TRIALS trial_result · 2014-11-18Clinical Trial Update: Efficacy of Bucelipase Alfa (BSSL) in Patients With Cystic Fibrosis and Pancreatic Insufficiency [Phase 2]
Phase 2 trial results evaluating Bucelipase alfa (BSSL) in cystic fibrosis patients with exocrine pancreatic insufficiency. Results were pos…
-
CLINICAL_TRIALS trial_result · 2014-11-14Clinical Trial Update: Nasally Delivered Pulmozyme for Sinusitis in Cystic Fibrosis [Phase 2]
Phase 2 clinical trial evaluating a nasally delivered Pulmozyme (dornase alfa) for sinusitis in cystic fibrosis; the study completed and res…