Congenital Myotonic Dystrophy
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2025-09-11Clinical Trial Update: Efficacy and Safety of Tideglusib in Congenital Myotonic Dystrophy [Phase 2, Phase 3]
Phase 2/3 clinical trial assessing the efficacy and safety of tideglusib in congenital myotonic dystrophy has completed with results posted.
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CLINICAL_TRIALS research · 2025-08-13Clinical Trial Update: Tideglusib: Expanded Access Use in Congenital Myotonic Dystrophy
This clinical trial update reports expanded access use of Tideglusib for congenital myotonic dystrophy, sponsored by AMO Pharma Limited, and…
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CLINICAL_TRIALS research · 2025-06-11Clinical Trial Update: DMCRN-02-001: Assessing Pediatric Endpoints in DM1
A clinical trial (DMCRN-02-001) assessing pediatric endpoints in congenital myotonic dystrophy (DM1) is currently recruiting.
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CLINICAL_TRIALS research · 2025-03-11Clinical Trial Update: Trial Readiness and Endpoint Assessment in Congenital Myotonic Dystrophy
This clinical trial update describes trial readiness and endpoint assessment for congenital myotonic dystrophy, sponsored by Virginia Common…
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CLINICAL_TRIALS research · 2024-11-21Clinical Trial Update: Myotonic Dystrophy Family Registry
A clinical trial registry entry for the Myotonic Dystrophy Family Registry, currently recruiting to collect data on myotonic dystrophy types…
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CLINICAL_TRIALS trial_result · 2024-07-05Clinical Trial Update: Trial Readiness and Endpoint Assessment in Congenital and Childhood Myotonic Dystrophy
Completed clinical trial update focusing on trial readiness and endpoint assessment in congenital and childhood myotonic dystrophy.