Congenital Amegakaryocytic Thrombocytopenia
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CLINICAL_TRIALS trial_result · 2026-03-09Clinical Trial Update: Treosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of Bone Marrow Failure Diseases (BMT CTN 1904) [Phase 2]
This update reports the completion of a Phase 2 study evaluating a treosulfan-based conditioning regimen before bone marrow or blood stem ce…
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CLINICAL_TRIALS trial_result · 2013-05-16Clinical Trial Update: Alemtuzumab, Fludarabine, and Busulfan Followed By Donor Stem Cell Transplant in Treating Young Patients With Hematologic Disorders [Phase 2]
Phase 2 trial evaluating a conditioning regimen of alemtuzumab, fludarabine, and busulfan followed by donor stem cell transplant in young pa…
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CLINICAL_TRIALS trial_result · 2012-11-12Clinical Trial Update: Busulfan, Antithymocyte Globulin, and Fludarabine Followed By a Donor Stem Cell Transplant in Treating Young Patients With Blood Disorders, Bone Marrow Disorders, Chronic Myelogenous Leukemia in First Chronic Phase, or Acute Myeloid Leukemia in First Remission [Phase 1, Phase 2]
This completed Phase 1/2 trial from UCSF evaluated a conditioning regimen of busulfan, antithymocyte globulin, and fludarabine followed by d…
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CLINICAL_TRIALS trial_result · 2012-11-12Clinical Trial Update: Donor Stem Cell Transplant in Treating Young Patients With Myelodysplastic Syndrome, Leukemia, Bone Marrow Failure Syndrome, or Severe Immunodeficiency Disease [Phase 1]
Phase 1 trial evaluating donor stem cell transplantation in young patients with congenital amegakaryocytic thrombocytopenia, leukemia, myelo…