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CLINICAL_TRIALS ClinicalTrials.gov record update

Hematopoietic Cell Transplantation Using Treosulfan-Based Conditioning for the Treatment of Bone Marrow Failure Diseases

This page presents selected fields from the linked source record. It does not add a medical interpretation.

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Record identity and dates

Source
ClinicalTrials.gov
Source record ID
NCT04965597
Title field or adapter rule
protocolSection.identificationModule.officialTitle
Ingested At
2026-04-25T22:28:16.054117+00:00
Published At
2026-03-09T00:00:00+00:00
Record Updated At
2026-03-09
Timestamp Basis
source retrieval time was not retained by the feed adapter
Date limitation
source retrieval time was not retained by the feed adapter

Fields recorded by this source

protocolSection.conditionsModule.conditions
["Bone Marrow Failure Syndrome", "Congenital Amegakaryocytic Thrombocytopenia", "Diamond-Blackfan Anemia", "Hereditary Sideroblastic Anemia", "Paroxysmal Nocturnal Hemoglobinuria", "Shwachman-Diamond Syndrome", "Hematologic Neoplasm With Germline GATA2 Mutation", "Hematologic Neoplasm With Germline SAMD9 Mutation", "Hematologic Neoplasm With Germline SAMD9L Mutation"]
protocolSection.statusModule.lastUpdatePostDateStruct.date
"2026-03-09"
protocolSection.identificationModule.nctId
"NCT04965597"
protocolSection.identificationModule.officialTitle
"Hematopoietic Cell Transplantation Using Treosulfan-Based Conditioning for the Treatment of Bone Marrow Failure Diseases"
protocolSection.statusModule.overallStatus
"COMPLETED"
protocolSection.designModule.phases
["PHASE2"]
protocolSection.statusModule.resultsFirstPostDateStruct.date
""

Study condition terms

  • Bone Marrow Failure Syndrome (protocolSection.conditionsModule.conditions)
  • Congenital Amegakaryocytic Thrombocytopenia (protocolSection.conditionsModule.conditions)
  • Diamond-Blackfan Anemia (protocolSection.conditionsModule.conditions)
  • Hereditary Sideroblastic Anemia (protocolSection.conditionsModule.conditions)
  • Paroxysmal Nocturnal Hemoglobinuria (protocolSection.conditionsModule.conditions)
  • Shwachman-Diamond Syndrome (protocolSection.conditionsModule.conditions)
  • Hematologic Neoplasm With Germline GATA2 Mutation (protocolSection.conditionsModule.conditions)
  • Hematologic Neoplasm With Germline SAMD9 Mutation (protocolSection.conditionsModule.conditions)
  • Hematologic Neoplasm With Germline SAMD9L Mutation (protocolSection.conditionsModule.conditions)

Intervention details are not present in the imported fields for this record. No drug-condition relationship is inferred from co-listing.

This index keeps the source fields it imported; it may not contain the complete original record. Verify wording and context in the linked source.