Congenital Adrenal Hyperplasia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-04-24Clinical Trial Update: Natural History Study of Patients With Excess Androgen
A NICHD-sponsored natural history study examining excess androgen in congenital adrenal hyperplasia and familial male-limited precocious pub…
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CLINICAL_TRIALS research · 2026-04-17Clinical Trial Update: Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Crinecerfont in Participants With Classic Congenital Adrenal Hyperplasia (CAH) Who Are Less Than 4 Years Old [Phase 2]
A Phase 2 clinical trial evaluating the safety, tolerability, and pharmacokinetics/pharmacodynamics of crinecerfont in children under 4 with…
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CLINICAL_TRIALS research · 2026-04-08Clinical Trial Update: A Study in Pediatric Participants With Congenital Adrenal Hyperplasia (Balance-CAH) [Phase 2, Phase 3]
A pediatric Phase 2/3 clinical trial evaluating Crinecerfont for congenital adrenal hyperplasia (classic CAH) is currently recruiting.
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CLINICAL_TRIALS research · 2026-03-27Clinical Trial Update: Parenting and CAH - 21-hydroxylase Deficiency
This clinical trial update shows that NCT06900153 in Paris is currently recruiting to study parenting in families affected by congenital adr…
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CLINICAL_TRIALS research · 2026-03-24Clinical Trial Update: A Study to Evaluate Atumelnant in Adults With Congenital Adrenal Hyperplasia [Phase 3]
This clinical trial update shows a Phase 3 study evaluating Atumelnant in adults with congenital adrenal hyperplasia, including the classic …
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CLINICAL_TRIALS research · 2026-03-20Clinical Trial Update: Pharmacokinetics, Safety and Tolerability of Crinecerfont in Participants With Congenital Adrenal Hyperplasia Who Are Less Than 2 Years Old [Phase 2]
A Phase 2 clinical trial update evaluating the pharmacokinetics, safety and tolerability of Crinecerfont in infants under 2 years with conge…
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CLINICAL_TRIALS research · 2026-03-16Clinical Trial Update: Syndromes With Neonatal Salt Loss: Not Only Congenital Adrenal Hyperplasia Due to 21-hydroxylase Deficiency (21OH-ISC)
A clinical trial investigating syndromes causing neonatal salt loss beyond congenital adrenal hyperplasia due to 21-hydroxylase deficiency i…
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CLINICAL_TRIALS research · 2026-03-09Clinical Trial Update: A Trial of Lu AG13909 in Participants With Congenital Adrenal Hyperplasia [Phase 1, Phase 2]
A Phase 1/Phase 2 clinical trial of Lu AG13909 for congenital adrenal hyperplasia is currently recruiting.
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CLINICAL_TRIALS research · 2025-12-23Clinical Trial Update: A Study of Gene Therapy for Classic Congenital Adrenal Hyperplasia (CAH) [Phase 1, Phase 2]
A status update for an ongoing Phase 1/2 gene therapy study for classic congenital adrenal hyperplasia, sponsored by Adrenas Therapeutics In…
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CLINICAL_TRIALS research · 2025-12-11Clinical Trial Update: Prenatal Dex Study [NA]
Clinical trial NCT02795871 evaluating prenatal dexamethasone for congenital adrenal hyperplasia has completed.
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CLINICAL_TRIALS research · 2025-09-23Clinical Trial Update: An Extension Study to Evaluate Safety and Efficacy in Participants Treated With CRN04894 [Phase 2]
Extension phase 2 clinical trial to assess safety and efficacy of CRN04894 in participants with congenital adrenal hyperplasia; currently re…
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CLINICAL_TRIALS research · 2025-09-16Clinical Trial Update: Congenital Adrenal Hyperplasia Once Daily Hydrocortisone Treatment [Phase 4]
A Phase 4 clinical trial is evaluating once-daily hydrocortisone for congenital adrenal hyperplasia, with recruitment currently ongoing.
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CLINICAL_TRIALS research · 2025-08-01Clinical Trial Update: Fertility And Sexual Function In CAH: CALLIOPE
A CALLIOPE study evaluating fertility and sexual function in congenital adrenal hyperplasia is currently recruiting, sponsored by the Univer…
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CLINICAL_TRIALS research · 2024-12-31Clinical Trial Update: Electronic Registry of Male Patients With Congenital Adrenal Hyperplasia 21-hydroxylase Deficiency
Clinical trial registry update indicating ongoing recruitment for male patients with congenital adrenal hyperplasia due to 21-hydroxylase de…
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CLINICAL_TRIALS research · 2024-08-21Clinical Trial Update: Testicular Adrenal Rest Tumor in Congenital Adrenal Hyperplasia Patients Attending Assuit University Children Hospital
A clinical trial at Assiut University investigates testicular adrenal rest tumor in patients with congenital adrenal hyperplasia. The study …
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CLINICAL_TRIALS research · 2016-12-21Clinical Trial Update: Continuous Subcutaneous Hydrocortisone Infusion in Congenital Adrenal Hyperplasia [Phase 2]
An update on a Phase 2 clinical trial evaluating continuous subcutaneous hydrocortisone infusion for congenital adrenal hyperplasia. The sni…
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CLINICAL_TRIALS research · 2016-09-29Clinical Trial Update: Adrenocortical Functions in Women With Nonclassical 21-hydroxylase Deficiency. [NA]
An update on a clinical trial evaluating adrenocortical function in women with nonclassical 21-hydroxylase deficiency, a form of congenital …
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CLINICAL_TRIALS research · 2015-09-17Clinical Trial Update: COrticosteroid in Congenital Adrenal Hyperplasia [Phase 2, Phase 3]
A clinical trial update for a corticosteroid therapy being evaluated in congenital adrenal hyperplasia, spanning Phase 2 and Phase 3. The cu…
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CLINICAL_TRIALS research · 2012-08-17Clinical Trial Update: Clinical Evaluation of NeoPlex4 Assay and NeoPlex System
This update notes the completed clinical evaluation of Luminex's NeoPlex4 Assay and NeoPlex System, assessing tests for congenital adrenal h…
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CLINICAL_TRIALS research · 2009-11-09Clinical Trial Update: Qualitative Research on Women With Congenital Adrenal Hyperplasia
Completed clinical trial reporting qualitative research findings on women with congenital adrenal hyperplasia.
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CLINICAL_TRIALS research · 2009-06-02Clinical Trial Update: Role of the Protein Osteoprotegerin in the Bone Health of Women With Congenital Adrenal Hyperplasia
A clinical trial update exploring the role of osteoprotegerin in bone health among women with congenital adrenal hyperplasia.
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CLINICAL_TRIALS research · 2008-12-09Clinical Trial Update: Determining the Long-Term Effects of Prenatal Dexamethasone Treatment in Children With 21-Hydroxylase Deficiency and Their Mothers
This clinical trial update focuses on the long-term effects of treating fetuses at risk for 21-hydroxylase congenital adrenal hyperplasia wi…