Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS research · 2025-12-23

Clinical Trial Update: A Study of Gene Therapy for Classic Congenital Adrenal Hyperplasia (CAH) [Phase 1, Phase 2]

View source ↗

Summary

A status update for an ongoing Phase 1/2 gene therapy study for classic congenital adrenal hyperplasia, sponsored by Adrenas Therapeutics Inc.

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Drugs mentioned

  • Gene Therapy for Classic Congenital Adrenal Hyperplasia

Snippet

Sponsor: Adrenas Therapeutics Inc | Conditions: Congenital Adrenal Hyperplasia | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING