Combined L-2-hydroxyglutaric Aciduria
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CLINICAL_TRIALS research · 2025-08-15Clinical Trial Update: An Individual Patient, Open Label Study to Use ACER-001 to Treat Combined D,L-2 Hydroxyglutaric Aciduria (C-2HGA) [Phase 1]
Clinical trial update indicating an individualized, open-label Phase 1 study of ACER-001 for Combined D,L-2-hydroxyglutaric aciduria is curr…