Clinical Trial Update: An Individual Patient, Open Label Study to Use ACER-001 to Treat Combined D,L-2 Hydroxyglutaric Aciduria (C-2HGA) [Phase 1]

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Summary

Clinical trial update indicating an individualized, open-label Phase 1 study of ACER-001 for Combined D,L-2-hydroxyglutaric aciduria is currently enrolling by i…

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Diseases / indications

• Combined L-2-hydroxyglutaric Aciduria

Drugs mentioned

• ACER-001 (sodium phenylbutyrate)

Snippet

Sponsor: Jerry Vockley, MD, PhD | Conditions: Combined D,L-2-hydroxyglutaric Aciduria | Phase 1 | Status: ENROLLING_BY_INVITATION