Charcot-marie-tooth Disease Type 1a
📧 Sign up to get email alerts when something new happens for Charcot-marie-tooth Disease Type 1a.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2026-04-21Clinical Trial Update: A First in Human Study to Assess the Safety, Tolerability, and Pharmacokinetics of EDK060 in Adults With CMT1A. [Phase 1]
A first-in-human Phase 1 trial is planned to assess the safety, tolerability, and pharmacokinetics of the investigational therapy EDK060 in …
-
CLINICAL_TRIALS research · 2026-04-13Clinical Trial Update: A Multi-omic Approach to the Identification of Novel Biomarkers in Early Charcot-Marie-Tooth 1A Disease (CMT1A)
This clinical trial investigates multi-omic approaches to identify novel biomarkers in early Charcot-Marie-Tooth disease type 1A (CMT1A) and…
-
CLINICAL_TRIALS research · 2026-03-10Clinical Trial Update: Studying Nerve Function and Structure in Charcot-Marie-Tooth Disease, Anti-MAG Neuropathy and CIDP
This clinical trial update indicates ongoing recruitment for a study evaluating nerve function and structure in Charcot-Marie-Tooth disease …
-
CLINICAL_TRIALS research · 2026-03-09Clinical Trial Update: Longitudinal Biomarkers With Selected Outcome Measures In CMT
A recruiting clinical trial aims to investigate longitudinal biomarkers and selected outcome measures in Charcot-Marie-Tooth disease, includ…
-
CLINICAL_TRIALS trial_result · 2025-12-23Clinical Trial Update: Evaluate the Safety and Efficacy of EN001 in Patients With Charcot-Marie-Tooth Disease Type 1A [Phase 1]
Phase 1 study evaluating EN001 for Charcot-Marie-Tooth disease type 1A has completed. The trial assessed safety and potential efficacy in pa…
- Want full summaries, importance scores, and drug timelines? Upgrade to Plus or Pro.
-
CLINICAL_TRIALS research · 2025-10-07Clinical Trial Update: Genetics of Charcot Marie Tooth (CMT) - Modifiers of CMT1A, New Causes of CMT2
Ongoing genetics study recruiting participants to identify modifiers of Charcot-Marie-Tooth disease, focusing on CMT1A modifiers and new cau…
-
CLINICAL_TRIALS research · 2025-07-03Clinical Trial Update: Identification of Novel Biomarkers in Early Charcot-Marie-Tooth 1A Disease [NA]
This clinical trial update describes ongoing efforts to identify novel biomarkers in early Charcot-Marie-Tooth disease type 1A.
-
CLINICAL_TRIALS research · 2025-06-27Clinical Trial Update: Tools for Therapeutic Evaluation in Charcot-Marie-Tooth Disease Type 1A: Outcome Measures and Biomarkers [NA]
Clinical trial update describing tools for therapeutic evaluation in Charcot-Marie-Tooth disease type 1A, focusing on outcome measures and b…
-
CLINICAL_TRIALS trial_result · 2025-06-24Clinical Trial Update: Phase I/IIa Trial of scAAV1.tMCK.NTF3 for Treatment of CMT1A [Phase 1, Phase 2]
Phase I/IIa trial update of scAAV1.tMCK.NTF3 for Charcot-Marie-Tooth disease type 1A. The study is not yet recruiting.
-
CLINICAL_TRIALS research · 2025-05-31Clinical Trial Update: Longitudinal Quantitative Neuromuscular MRI in Neuropathic Patients [NA]
This clinical trial is evaluating longitudinal quantitative neuromuscular MRI in patients with neuropathies and is currently recruiting.
-
CLINICAL_TRIALS trial_result · 2025-05-29Clinical Trial Update: The Safety and Tolerability of Engensis (VM202) in Patients With Charcot-Marie-Tooth Disease Subtype 1A (CMT1A) [Phase 1, Phase 2]
Phase 1/2 trial evaluating Engensis (VM202) safety and tolerability in Charcot-Marie-Tooth disease type 1A (CMT1A) has completed and results…
-
CLINICAL_TRIALS trial_result · 2025-01-09Clinical Trial Update: A Study to Assess the Efficacy and Safety of PXT3003 in Charcot-Marie-Tooth Type 1A [Phase 3]
Phase 3 study evaluating PXT3003 in Charcot-Marie-Tooth disease type 1A has completed. The document summarizes the completion status of the …
-
CLINICAL_TRIALS trial_result · 2024-12-27Clinical Trial Update: Fall Risk Assessment in a Population of Charcot-Marie-Tooth Disease Type 1A (CMT 1A) by Timed Up and Go Test [NA]
A completed clinical trial evaluating fall risk in patients with Charcot-Marie-Tooth disease type 1A using the Timed Up and Go test.
-
CLINICAL_TRIALS trial_result · 2024-02-20Clinical Trial Update: Assessing Long Term Safety and Tolerability of PXT3003 in Patients With Charcot-Marie-Tooth Disease Type 1A [Phase 3]
Phase 3 clinical trial update evaluating long-term safety and tolerability of PXT3003 in Charcot-Marie-Tooth disease type 1A.
-
CLINICAL_TRIALS trial_result · 2020-11-02Clinical Trial Update: SERENDEM : MD1003 in Patients Suffering From Demyelinating Neuropathies, an Open Label Pilot Study [Phase 2]
Phase 2 open-label pilot study of MD1003 (serendem) in demyelinating neuropathies completed with results posted.
-
CLINICAL_TRIALS trial_result · 2020-02-27Clinical Trial Update: Phase III Trial Assessing the Efficacy and Safety of PXT3003 in CMT1A Patients (PLEO-CMT) [Phase 3]
Phase III trial update for PXT3003 in Charcot-Marie-Tooth Disease Type 1A (PLEO-CMT) has completed with results posted in 2020.
-
CLINICAL_TRIALS research · 2019-01-22Clinical Trial Update: Effect of Orthoses and Underfoot Vibration on Balance in Neuropathy
This clinical trial update describes a study evaluating whether foot orthoses and underfoot vibration affect balance in people with Charcot-…
-
CLINICAL_TRIALS trial_result · 2017-03-10Clinical Trial Update: Driving Ability in Patients With CMT 1A [NA]
A completed clinical trial update assessing driving ability in patients with Charcot-Marie-Tooth disease type 1A. The snippet notes status a…
-
CLINICAL_TRIALS trial_result · 2017-02-16Clinical Trial Update: Phase II, Randomized, Placebo-controlled Trial in Patients With Charcot-marie-tooth Disease Type 1A [Phase 2]
Phase II randomized, placebo-controlled trial in Charcot-Marie-Tooth disease type 1A completed; results were posted in 2017.
-
CLINICAL_TRIALS trial_result · 2013-03-06Clinical Trial Update: High Dose Ascorbic Acid Treatment of CMT1A [Phase 2, Phase 3]
A clinical trial evaluating high-dose ascorbic acid for Charcot-Marie-Tooth disease type 1A has completed Phase 2 and Phase 3 stages.
-
CLINICAL_TRIALS research · 2011-02-04Clinical Trial Update: Treadmill, Stretching and Proprioceptive Exercise (TreSPE) Rehabilitation Program for Charcot-Marie-Tooth Neuropathy Type 1A (CMT1A) [Phase 2, Phase 3]
This entry reports a Phase 2/Phase 3 clinical trial update for the TreSPE rehabilitation program in Charcot-Marie-Tooth disease type 1A, wit…