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CLINICAL_TRIALS trial_result · 2025-12-23

Clinical Trial Update: Evaluate the Safety and Efficacy of EN001 in Patients With Charcot-Marie-Tooth Disease Type 1A [Phase 1]

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Summary

Phase 1 study evaluating EN001 for Charcot-Marie-Tooth disease type 1A has completed. The trial assessed safety and potential efficacy in patients with CMT1A.

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Diseases / indications

Drugs mentioned

  • EN001

Snippet

Sponsor: ENCell | Conditions: Charcot-Marie-Tooth Disease Type 1A | Phase 1 | Status: COMPLETED